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Pag-aaral pangklinika para sa Rare Diseases sa California
10 pag-aaral para sa Rare Diseases ang naghahanap ng mga kalahok sa mga site sa California.
Mga Lungsod sa California
Opisyal na teksto ng pag-aaral (English)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of California, Los Angeles, Los Angeles
- University of California, Irvine Medical Center, Orange
- Stanford University, Stanford
- at 2 pa
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 100 Years · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT02450851A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
- The University of California, Los Angeles (UCLA), Los Angeles
Nagre-recruitPhase 1
Edad 18 hanggang 40 · Lahat ng kasarian · Na-update Set 29, 2026 · NCT07180355A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia
- University of California - San Francisco, San Francisco
Nagre-recruitPhase 1/2
Edad 18 hanggang 65 · Lahat ng kasarian · Na-update Set 21, 2026 · NCT06525636Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- UCLA Ataxia Center, Los Angeles
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Lahat ng edad · Lahat ng kasarian · Na-update Set 1, 2026 · NCT06016946International Rare Brain Tumor Registry
- Children's Hospital Los Angeles, Los Angeles
- University of California San Francisco, San Francisco
Nagre-recruitObservasyonal na pag-aaral
Hanggang edad 45 · Lahat ng kasarian · Na-update Ago 7, 2026 · NCT05697874Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of California - Irvine Medical Center, Irvine
Nagre-recruitPhase 2
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT07123155A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
- UCSF Benioff Children's Hospital Oakland, Oakland
Nagre-recruitPhase 1/2
30 Months · Lahat ng kasarian · Na-update Abr 17, 2026 · NCT04998396The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- Children's Hospital of Orange County, Orange
- UC Irvine, Orange
- UC Davis, Sacramento
Nagre-recruitPhase 2
Edad 12 pataas · Lahat ng kasarian · Na-update Hul 1, 2025 · NCT04372615Prospective Observational International Registry of Patients With Newly Diagnosed Peripheral T Cell Lymphoma.
- Stanford University, Stanford
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update May 6, 2025 · NCT03964480Epilepsy Learning Healthcare System (ELHS)
- Children's Hospital Los Angeles, Los Angeles
- University of Southern California, Los Angeles
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ago 30, 2024 · NCT06265103Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.