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Pag-aaral pangklinika para sa Rare Diseases sa Pennsylvania
7 pag-aaral para sa Rare Diseases ang naghahanap ng mga kalahok sa mga site sa Pennsylvania.
Mga Lungsod sa Pennsylvania
Opisyal na teksto ng pag-aaral (English)
A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
Nagre-recruitPhase 1
Edad 18 hanggang 40 · Lahat ng kasarian · Na-update Nob 6, 2026 · NCT07180355Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Pennsylvania, Philadelphia
- Children's Hospital of Philadelphia, Philadelphia
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
1 Month – 100 Years · Lahat ng kasarian · Na-update Nob 3, 2026 · NCT02450851Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Children's Hospital of Philadelphia, Philadelphia
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Lahat ng edad · Lahat ng kasarian · Na-update Set 1, 2026 · NCT06016946Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
Nagre-recruitPhase 2
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 23, 2026 · NCT07123155A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
- University of Pennsylvania, Philadelphia
- University of Pittsburg, Pittsburgh
Nagre-recruitPhase 1/2
Edad 25 hanggang 65 · Lahat ng kasarian · Na-update May 5, 2026 · NCT06826612The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- University of Pennsylvania, Philadelphia
- University of Pittsburgh, Pittsburgh
Nagre-recruitPhase 2
Edad 12 pataas · Lahat ng kasarian · Na-update Hul 1, 2025 · NCT04372615Epilepsy Learning Healthcare System (ELHS)
- Penn State Hershey, Hershey
- Children's Hospital of Philadelphia (CHOP), Philadelphia
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ago 30, 2024 · NCT06265103Mula sa ClinicalTrials.gov, na-kuha noong Nob 15, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.