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Pag-aaral pangklinika para sa Sickle Cell Disease sa Massachusetts
10 pag-aaral para sa Sickle Cell Disease ang naghahanap ng mga kalahok sa mga site sa Massachusetts.
Mga Lungsod sa Massachusetts
Opisyal na teksto ng pag-aaral (English)
A Study to Evaluate How Well Etavopivat Works in People With Sickle Cell Disease
- Boston Children's Hospital, Boston
- Boston Medical Center, Boston
Nagre-recruitPhase 3
Edad 12 pataas · Lahat ng kasarian · Na-update Set 17, 2026 · NCT06612268A Phase I/II Study of ITU512 in Healthy Participants and Patients With Sickle Cell Disease
- Boston Childrens Hospital, Boston
Nagre-recruitPhase 1/2Malugod na tinatanggap ang malusog na boluntaryo
Edad 12 hanggang 55 · Lahat ng kasarian · Na-update Set 9, 2026 · NCT06546670A Study to Evaluate BMS-986470 in Healthy Volunteers and Participants With Sickle Cell Disease
- Local Institution - 0024, Boston
- Boston Medical Center, Boston
Nagre-recruitPhase 1/2Malugod na tinatanggap ang malusog na boluntaryo
Edad 18 pataas · Lahat ng kasarian · Na-update Ago 18, 2026 · NCT06481306ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders
- Massachusetts General Hospital Comprehensive Hemophilia and Thrombosis Treatment Center, Boston
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ago 17, 2026 · NCT04398628Comparing the Effectiveness of Matched Related Donor Hematopoietic Stem Cell Transplantation to Disease Modifying Therapy in Pediatric Patients With Sickle Cell Disease
- Boston Children's Hospital (MRD-HCT), Boston
- Boston Children's Hospital (NT-DMT), Boston
Nagre-recruitObservasyonal na pag-aaral
Edad 3 hanggang 20 · Lahat ng kasarian · Na-update Hun 4, 2026 · NCT06941389Promoting Resilience Among Adolescents and Young Adults With Sickle Cell Disease
- Boston Children's Hospital, Boston
Nagre-recruit
Edad 8 hanggang 25 · Lahat ng kasarian · Na-update May 5, 2026 · NCT06555939Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
- Boston Children's Hospital, Boston
Nagre-recruitPhase 1
Edad 13 hanggang 40 · Lahat ng kasarian · Na-update Peb 3, 2026 · NCT06647979A Long-term Follow-up Study in Patients Who Received BEAM-101
- Boston Children's Hospital, Boston
Nagre-recruitObservasyonal na pag-aaral
Edad 14 hanggang 37 · Lahat ng kasarian · Na-update Ene 28, 2026 · NCT07373639A Pilot Study on Neuroimaging in SCD: Part of The Boston Consortium to Cure Sickle Cell Disease
- Boston Children's Hospital, Boston
Nagre-recruitObservasyonal na pag-aaral
Edad 8 hanggang 18 · Lahat ng kasarian · Na-update Dis 12, 2025 · NCT04166526Study of the Role of Genetic Modifiers in Hemoglobinopathies
- Boston Children's Hospital, Boston
Nagre-recruitObservasyonal na pag-aaral
Edad 2 pataas · Lahat ng kasarian · Na-update Mar 20, 2024 · NCT05799118Mula sa ClinicalTrials.gov, na-kuha noong Okt 1, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.