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Pag-aaral pangklinika para sa Spinal Muscular Atrophy sa Massachusetts
6 pag-aaral para sa Spinal Muscular Atrophy ang naghahanap ng mga kalahok sa mga site sa Massachusetts.
Mga Lungsod sa Massachusetts
Opisyal na teksto ng pag-aaral (English)
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Nagre-recruitPhase 2
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07287982A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Boston Children's Hospital, Boston
Nagre-recruitPhase 1
Edad 3 pataas · Lahat ng kasarian · Na-update Set 3, 2026 · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Boston Children's Hospital, Boston
Nagre-recruit
Edad 3 pataas · Lahat ng kasarian · Na-update Ago 19, 2026 · NCT05866419ALS/MND Natural History Study Data Repository
- Lahey Clinic, Burlington
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 90 · Lahat ng kasarian · Na-update May 20, 2026 · NCT05966038Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
- Boston Children's Hospital, Boston
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Abr 9, 2026 · NCT06839469A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
- Boston Children's Hospital, Boston
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 54 · Kababaihan · Na-update Mar 9, 2026 · NCT05789758Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.