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Pag-aaral pangklinika para sa Spinal Muscular Atrophy na nagre-recruit sa U.S.
23 pag-aaral para sa Spinal Muscular Atrophy ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.
Mga lungsod na may pinakamaraming pag-aaral
- Mountain View, CA9 pag-aaral
- New York City, NY9 pag-aaral
- Philadelphia, PA7 pag-aaral
- Chicago, IL6 pag-aaral
- Norfolk, VA6 pag-aaral
- Grand Rapids, MI6 pag-aaral
- Boston, MA5 pag-aaral
- Houston, TX5 pag-aaral
- Lewisville, TX4 pag-aaral
- Little Rock, AR4 pag-aaral
- Phoenix, AZ4 pag-aaral
- Aurora, CO4 pag-aaral
- Memphis, TN3 pag-aaral
- Durham, NC3 pag-aaral
- Orlando, FL3 pag-aaral
- Cedar Rapids, IA3 pag-aaral
- Columbia, MO3 pag-aaral
- Harrisburg, PA3 pag-aaral
- Charlottesville, VA3 pag-aaral
- Minneapolis, MN3 pag-aaral
- Portland, OR3 pag-aaral
- Fort Worth, TX3 pag-aaral
- Dallas, TX3 pag-aaral
- Gainesville, FL3 pag-aaral
- Atlanta, GA3 pag-aaral
- Orange, CA3 pag-aaral
Ayos sa estado
- Arizona4 pag-aaral
- Arkansas4 pag-aaral
- California11 pag-aaral
- Colorado4 pag-aaral
- Florida8 pag-aaral
- Georgia3 pag-aaral
- Illinois6 pag-aaral
- Iowa3 pag-aaral
- Massachusetts6 pag-aaral
- Michigan6 pag-aaral
- Minnesota3 pag-aaral
- Missouri4 pag-aaral
- New York10 pag-aaral
- North Carolina3 pag-aaral
- Oregon3 pag-aaral
- Pennsylvania8 pag-aaral
- Tennessee3 pag-aaral
- Texas10 pag-aaral
- Virginia7 pag-aaral
Mga pag-aaral na kamakailan lamang in-update
Opisyal na teksto ng pag-aaral (English)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
Nagre-recruitPhase 4
3 Months – 24 Months · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT05861986A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Nagre-recruitPhase 2
Hanggang edad 2 · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT07047144A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam
Nagre-recruitPhase 3
Edad 15 hanggang 60 · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT07444476A Registry of Cases of Spinal Muscular Atrophy
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Set 30, 2026 · NCT07805278ASsessing The REAl-world Safety & Effectiveness of Spinal Muscular Atrophy Participants Treated With Intrathecal Onasemnogene Abeparvovec-brve (OAV101B) (ITVISMA®): A U.S. Pragmatic Multicenter Study (STREAM)
Nagre-recruitPhase 4
Edad 2 hanggang 100 · Lahat ng kasarian · Na-update Set 18, 2026 · NCT07448610A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
Nagre-recruitPhase 2
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
Nagre-recruitPhase 4
3 Months – 24 Months · Lahat ng kasarian · Na-update Set 10, 2026 · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
Nagre-recruitPhase 1
Edad 3 pataas · Lahat ng kasarian · Na-update Set 3, 2026 · NCT06555419Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)
Nagre-recruit
Edad 18 hanggang 80 · Lahat ng kasarian · Na-update Set 2, 2026 · NCT07521930Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
Nagre-recruit
Edad 3 pataas · Lahat ng kasarian · Na-update Ago 19, 2026 · NCT05866419A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)
Nagre-recruitPhase 3
0 Days – 42 Days · Lahat ng kasarian · Na-update Ago 18, 2026 · NCT07221669A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec
Nagre-recruitPhase 3
0 Days – 7 Months · Lahat ng kasarian · Na-update Ago 11, 2026 · NCT07444450Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies
Nagre-recruitObservasyonal na pag-aaral
Edad 5 hanggang 20 · Lahat ng kasarian · Na-update Hul 9, 2026 · NCT06532474Clinical Procedures to Support Research in ALS
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 15, 2026 · NCT03489278ALS/MND Natural History Study Data Repository
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 90 · Lahat ng kasarian · Na-update May 20, 2026 · NCT05966038Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
Nagre-recruitObservasyonal na pag-aaral
Edad 12 pataas · Lahat ng kasarian · Na-update May 14, 2026 · NCT06955897Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Abr 9, 2026 · NCT06839469HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness
Nagre-recruit
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT07488338Gait and Bone Health in SMA
Nagre-recruitObservasyonal na pag-aaral
Edad 8 hanggang 50 · Lahat ng kasarian · Na-update Mar 18, 2026 · NCT07400198Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
Nagre-recruit
Edad 18 pataas · Lahat ng kasarian · Na-update Mar 17, 2026 · NCT07478172A Study to Learn How Nusinersen (Spinraza) Affects Participants With Spinal Muscular Atrophy (SMA) Who Took it Before or During Pregnancy And About The Health of Their Babies
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 54 · Kababaihan · Na-update Mar 9, 2026 · NCT05789758Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System
Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Ene 16, 2026 · NCT07223489Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ene 31, 2025 · NCT04174157Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.