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Pag-aaral pangklinika para sa Spinal Muscular Atrophy na nagre-recruit sa U.S.

23 pag-aaral para sa Spinal Muscular Atrophy ang nagre-recruit ng mga kalahok sa mga site sa buong Estados Unidos.

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Opisyal na teksto ng pag-aaral (English)

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

Nagre-recruitPhase 2
Hanggang edad 2 · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT07047144

A Registry of Cases of Spinal Muscular Atrophy

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Set 30, 2026 · NCT07805278

Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)

Nagre-recruit
Edad 18 hanggang 80 · Lahat ng kasarian · Na-update Set 2, 2026 · NCT07521930

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Nagre-recruit
Edad 3 pataas · Lahat ng kasarian · Na-update Ago 19, 2026 · NCT05866419

Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies

Nagre-recruitObservasyonal na pag-aaral
Edad 5 hanggang 20 · Lahat ng kasarian · Na-update Hul 9, 2026 · NCT06532474

Clinical Procedures to Support Research in ALS

Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Hun 15, 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 90 · Lahat ng kasarian · Na-update May 20, 2026 · NCT05966038

Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

Nagre-recruitObservasyonal na pag-aaral
Edad 12 pataas · Lahat ng kasarian · Na-update May 14, 2026 · NCT06955897

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Nagre-recruitObservasyonal na pag-aaralMalugod na tinatanggap ang malusog na boluntaryo
Edad 5 pataas · Lahat ng kasarian · Na-update Abr 9, 2026 · NCT06839469

HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness

Nagre-recruit
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Mar 23, 2026 · NCT07488338

Gait and Bone Health in SMA

Nagre-recruitObservasyonal na pag-aaral
Edad 8 hanggang 50 · Lahat ng kasarian · Na-update Mar 18, 2026 · NCT07400198

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

Nagre-recruit
Edad 18 pataas · Lahat ng kasarian · Na-update Mar 17, 2026 · NCT07478172

Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System

Nagre-recruitObservasyonal na pag-aaral
Edad 18 pataas · Lahat ng kasarian · Na-update Ene 16, 2026 · NCT07223489

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ene 31, 2025 · NCT04174157

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.