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Pag-aaral pangklinika para sa Spinal Muscular Atrophy sa Michigan

6 pag-aaral para sa Spinal Muscular Atrophy ang naghahanap ng mga kalahok sa mga site sa Michigan.

Mga Lungsod sa Michigan

Opisyal na teksto ng pag-aaral (English)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • Helen DeVos Children's Hospital at Spectrum Health, Grand Rapids
Nagre-recruitPhase 4
3 Months – 24 Months · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT05861986

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • Helen DeVos Children's Hospital at Spectrum Health, Grand Rapids
Nagre-recruitPhase 2
Hanggang edad 2 · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT07047144

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • Helen DeVos Children's Hospital at Spectrum Health, Grand Rapids
Nagre-recruitPhase 4
3 Months – 24 Months · Lahat ng kasarian · Na-update Set 10, 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Helen DeVos Children's Hospita, Grand Rapids
Nagre-recruitPhase 1
Edad 3 pataas · Lahat ng kasarian · Na-update Set 3, 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Helen DeVos Children's Hospital, Grand Rapids
Nagre-recruit
Edad 3 pataas · Lahat ng kasarian · Na-update Ago 19, 2026 · NCT05866419

ALS/MND Natural History Study Data Repository

  • Henry Ford Health System, Detroit
  • Trinity Health Michigan, Grand Rapids
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 90 · Lahat ng kasarian · Na-update May 20, 2026 · NCT05966038

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.