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Pag-aaral pangklinika para sa Spinal Muscular Atrophy sa Missouri

4 pag-aaral para sa Spinal Muscular Atrophy ang naghahanap ng mga kalahok sa mga site sa Missouri.

Mga Lungsod sa Missouri

Opisyal na teksto ng pag-aaral (English)

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • The Curators of the University of Missouri on behalf of University of Missouri Health Care, Columbia
Nagre-recruitPhase 2
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07287982

ALS/MND Natural History Study Data Repository

  • Saint Louis University, St Louis
Nagre-recruitObservasyonal na pag-aaral
Edad 18 hanggang 90 · Lahat ng kasarian · Na-update May 20, 2026 · NCT05966038

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

  • NextGen Precision Health Building, Clinical and Translational Science Unit, Columbia
Nagre-recruit
Edad 18 pataas · Lahat ng kasarian · Na-update Mar 17, 2026 · NCT07478172

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • University of Missouri Health System, Columbia
  • Washington University School of Medicine in St. Louis, St Louis
Nagre-recruitObservasyonal na pag-aaral
Lahat ng edad · Lahat ng kasarian · Na-update Ene 31, 2025 · NCT04174157

Mula sa ClinicalTrials.gov, na-kuha noong Okt 5, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.