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Pag-aaral pangklinika para sa Spinal Muscular Atrophy sa Norfolk, VA

6 pag-aaral para sa Spinal Muscular Atrophy ang naghahanap ng mga kalahok sa mga site sa loob at paligid ng Norfolk (sa loob ng humigit-kumulang 30 milya). Buksan ang pag-aaral upang makita kung sino ang makakasali at kung paano makipag-ugnayan sa koponan ng pag-aaral.

Opisyal na teksto ng pag-aaral (English)

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A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety in Participants Aged 15 to 60 Years With Spinal Muscular Atrophy (SMA) Who Are Either New to SMA Treatment or Were Previously Treated With Risdiplam

Nagre-recruitPhase 3
  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
Edad 15 hanggang 60 · Lahat ng kasarian · Na-update Okt 2, 2026 · NCT07444476

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

Nagre-recruitPhase 2
  • Childrens Hospital of The Kings Daughters, Norfolk
Edad 5 hanggang 17 · Lahat ng kasarian · Na-update Set 14, 2026 · NCT07287982

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

Nagre-recruitPhase 1
  • Children's Hospital of the King's Daughters_Norfolk, Norfolk
Edad 3 pataas · Lahat ng kasarian · Na-update Set 3, 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

Nagre-recruit
  • Childrens Hospital of the King's Daughters, Norfolk
Edad 3 pataas · Lahat ng kasarian · Na-update Ago 19, 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

Nagre-recruitPhase 3
  • Childrens Hospital of the Kings Daughter Norfolk, Norfolk
0 Days – 42 Days · Lahat ng kasarian · Na-update Ago 18, 2026 · NCT07221669

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

Nagre-recruitObservasyonal na pag-aaral
  • Children's Hospital of The King's Daughters, Norfolk
Lahat ng edad · Lahat ng kasarian · Na-update Ene 31, 2025 · NCT04174157

Pag-aaral para sa Spinal Muscular Atrophy sa ibang lungsod

Iba pang pag-aaral sa Norfolk

Mula sa ClinicalTrials.gov, na-kuha noong Okt 6, 2026. Ang bawat pag-aaral ay may sariling pamantayan sa eligibility; ang koponan ng pag-aaral ang magdedesisyon kung sino ang makakasali.