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Essais cliniques pour Amyotrophie spinale dans Texas

10 études pour Amyotrophie spinale recherchent des participants dans Texas.

Villes dans Texas

Texte officiel de l'étude (anglais)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • The University of Texas Southwestern Medical Center at Dallas, Dallas
  • Cook Children's Jane and John Justin Neurosciences Center, Fort Worth
Recrutement en coursPhase 4
3 Months – 24 Months · Tous sexes · Mis à jour le 2 oct. 2026 · NCT05861986

A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy

  • University of Texas Southwestern Medical Center, Dallas
  • Neurology Rare Disease Center, Flower Mound
  • Cook Children's Medical Center, Fort Worth
  • et 1 autres
Recrutement en coursPhase 2
Jusqu'à 2 ans · Tous sexes · Mis à jour le 2 oct. 2026 · NCT07047144

A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy

  • Neurology Rare Disease Center, Flower Mound
  • Texas Children's Hospital, Houston
Recrutement en coursPhase 2
Âges de 5 à 17 · Tous sexes · Mis à jour le 14 sept. 2026 · NCT07287982

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Texas Southwestern Medical Center, Dallas
Recrutement en coursPhase 4
3 Months – 24 Months · Tous sexes · Mis à jour le 10 sept. 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Texas Childrens Hospital Houston, Houston
Recrutement en coursPhase 1
Âges de 3 ans et plus · Tous sexes · Mis à jour le 3 sept. 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Texas Children's Hospital, Houston
Recrutement en cours
Âges de 3 ans et plus · Tous sexes · Mis à jour le 19 août 2026 · NCT05866419

A Study to Learn About Salanersen's (BIIB115) Effects on Movement and Its Safety When Given Before Symptoms Appear in Babies With Genetically Diagnosed Spinal Muscular Atrophy (SMA)

  • Neurology Rare Disease Center, Flower Mound
Recrutement en coursPhase 3
0 Days – 42 Days · Tous sexes · Mis à jour le 18 août 2026 · NCT07221669

A Study to Learn About the Safety and Effects of Salanersen (BIIB115) When Given to Babies With Spinal Muscular Atrophy (SMA) Who Were Previously Treated With Onasemnogene Abeparvovec

  • Neurology Rare Disease Center, Flower Mound
Recrutement en coursPhase 3
0 Days – 7 Months · Tous sexes · Mis à jour le 11 août 2026 · NCT07444450

Clinical Procedures to Support Research in ALS

  • University of Texas San Antonio Health Science Center, San Antonio
Recrutement en coursÉtude observationnelle
Âges de 18 ans et plus · Tous sexes · Mis à jour le 15 juin 2026 · NCT03489278

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Cook Children's, Fort Worth
  • Texas Children's Hospital, Houston
  • CHRISTUS Health, San Antonio
Recrutement en coursÉtude observationnelle
Tous âges · Tous sexes · Mis à jour le 31 janv. 2025 · NCT04174157

Source : ClinicalTrials.gov, données récupérées le 5 oct. 2026. Chaque étude définit ses propres critères d'éligibilité ; l'équipe de l'étude décide qui peut y participer.