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Dachaigh › Beta-Thalassemia

Sgrùdaidhean clionaigeach Beta-Thalassemia a’ fastadh anns na SA

Tha 15 sgrùdaidhean airson Beta-Thalassemia a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

Bailtean leis na sgrùdaidhean as motha

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Sgrùdaidhean air an ùrachadh o chionn ghoirid

Teacsa sgrùdaidh oifigeil (Beurla)

Collection of Human Biospecimens for Basic and Clinical Research Into Globin Variants

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 2 Dàmh 2026 · NCT03937817

ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

A’ fastadhÌre 1/2
Aoisean 18 gu 40 · Gach gnè · Air ùrachadh 23 Sult 2026 · NCT06364774

Partial Stem Cell Transplant for Sickle Cell Disease From Matched Donors

A’ fastadhÌre 1/2
Aoisean 4 gu 65 · Gach gnè · Air ùrachadh 4 Sult 2026 · NCT07599176

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

A’ fastadhÌre 1/2
Aoisean 5 gu 40 · Gach gnè · Air ùrachadh 13 Lùna 2026 · NCT03653338

Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia

A’ fastadhÌre 2
Aoisean 6 gu 17 · Gach gnè · Air ùrachadh 10 Iuch 2026 · NCT04143724

MT2021-08T Cell Receptor Alpha/Beta Depletion PBSC Transplantation for Heme Malignancies

A’ fastadhÌre 2
Suas gu aois 60 · Gach gnè · Air ùrachadh 6 Gibl 2026 · NCT05735717

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

A’ fastadhÌre 1
Aoisean 13 gu 40 · Gach gnè · Air ùrachadh 3 Gearr 2026 · NCT06647979

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355

Study of Panobinostat (LBH589) in Patients With Sickle Cell Disease

A’ fastadhÌre 1
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 9 Faoi 2026 · NCT01245179

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

A’ fastadhÌre 2
1 Day – 30 Years · Gach gnè · Air ùrachadh 8 Lùna 2025 · NCT04099966

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 11 Gearr 2025 · NCT06271512

Study of the Role of Genetic Modifiers in Hemoglobinopathies

A’ fastadhSgrùdadh amharc
Aoisean 2 agus nas sine · Gach gnè · Air ùrachadh 20 Màrt 2024 · NCT05799118

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.