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Sgrùdaidhean clionaigeach Beta-Thalassemia ann an Pennsylvania

Tha 5 sgrùdaidhean airson Beta-Thalassemia a’ lorg phàirtichean aig làraichean ann an Pennsylvania.

Bailtean ann an Pennsylvania

Teacsa sgrùdaidh oifigeil (Beurla)

ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia

  • Children's Hospital of Philadelphia, Philadelphia
A’ fastadhÌre 1/2
Aoisean 18 gu 40 · Gach gnè · Air ùrachadh 23 Sult 2026 · NCT06364774

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

  • Children's Hospital of Pittsburgh of UPMC, Pittsburgh
A’ fastadhÌre 1/2
Aoisean 5 gu 40 · Gach gnè · Air ùrachadh 13 Lùna 2026 · NCT03653338

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

  • Children's Hospital of Philadelphia, Philadelphia
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 11 Gearr 2025 · NCT06271512

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.