Dachaigh › Beta-Thalassemia › Pennsylvania
Sgrùdaidhean clionaigeach Beta-Thalassemia ann an Pennsylvania
Tha 5 sgrùdaidhean airson Beta-Thalassemia a’ lorg phàirtichean aig làraichean ann an Pennsylvania.
Bailtean ann an Pennsylvania
Teacsa sgrùdaidh oifigeil (Beurla)
ALS20-101 Lentiviral Gene Therapy for Beta Thalassemia
- Children's Hospital of Philadelphia, Philadelphia
A’ fastadhÌre 1/2
Aoisean 18 gu 40 · Gach gnè · Air ùrachadh 23 Sult 2026 · NCT06364774T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias
- Children's Hospital of Pittsburgh of UPMC, Pittsburgh
A’ fastadhÌre 1/2
Aoisean 5 gu 40 · Gach gnè · Air ùrachadh 13 Lùna 2026 · NCT03653338Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
- Children's Hospital of Philadelphia, Philadelphia
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 11 Gearr 2025 · NCT06271512Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.