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Dachaigh › Dystrophy Fèithe Duchenne › California

Sgrùdaidhean clionaigeach Dystrophy Fèithe Duchenne ann an California

Tha 6 sgrùdaidhean airson Dystrophy Fèithe Duchenne a’ lorg phàirtichean aig làraichean ann an California.

Bailtean ann an California

Teacsa sgrùdaidh oifigeil (Beurla)

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

  • Loma Linda University Pediatric Subspecialty Clinics, Loma Linda
  • Children's Hospital Los Angeles, Los Angeles
  • Valley Children's Hospital, Madera
  • agus 2 a bharrachd
A’ fastadhSgrùdadh amharc
Aoisean 2 agus nas sine · Fir · Air ùrachadh 24 Sult 2026 · NCT06564974

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • University of California, San Diego, La Jolla
  • University of California, Los Angeles, Los Angeles
  • Stanford University, Palo Alto
  • agus 1 a bharrachd
A’ fastadhÌre 1
Aoisean 2 agus nas sine · Fir · Air ùrachadh 11 Sult 2026 · NCT04626674

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • UC Davis, Sacramento
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 28 Iuch 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • University of California, Los Angeles Medical Center, Los Angeles
  • University of California, Davis, Sacramento
  • University of California, San Diego
A’ fastadhÌre 1/2
Aoisean 0 gu 17 · Fir · Air ùrachadh 8 Iuch 2026 · NCT06138639

Duchenne Electronic Health Record Study

  • UC Davis Health, Sacramento
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 27 Cèit 2026 · NCT07609394

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 9 Gibl 2026 · NCT06839469

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.