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Sgrùdaidhean clionaigeach Dystrophy Fèithe Duchenne a’ fastadh anns na SA

Tha 26 sgrùdaidhean airson Dystrophy Fèithe Duchenne a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

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Teacsa sgrùdaidh oifigeil (Beurla)

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

A’ fastadhÌre 3
Aoisean 7 gu 11 · Fir · Air ùrachadh 28 Sult 2026 · NCT07160634

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

A’ fastadhSgrùdadh amharc
Aoisean 2 agus nas sine · Fir · Air ùrachadh 24 Sult 2026 · NCT06564974

Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy

A’ fastadhÌre 1
Aoisean 8 gu 18 · Fir · Air ùrachadh 24 Lùna 2026 · NCT07172971

The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy

A’ fastadhSgrùdadh amharc
0 Days – 3 Years · Fir · Air ùrachadh 19 Lùna 2026 · NCT07092540

Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients

A’ fastadh
Aoisean 6 agus nas sine · Fir · Air ùrachadh 17 Lùna 2026 · NCT07766980

Once Weekly Infant Corticosteroid Trial for DMD

A’ fastadhÌre 4
1 Month – 30 Months · Fir · Air ùrachadh 14 Lùna 2026 · NCT05412394

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 28 Iuch 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

A’ fastadhÌre 1/2
Aoisean 0 gu 17 · Fir · Air ùrachadh 8 Iuch 2026 · NCT06138639

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

A’ fastadhSgrùdadh amharc
Aoisean 6 agus nas sine · Gach gnè · Air ùrachadh 2 Iuch 2026 · NCT07127978

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

A’ fastadhÌre 1/2
Aoisean 2 gu 7 · Fir · Air ùrachadh 23 Ògmh 2026 · NCT07429240

Duchenne Electronic Health Record Study

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 27 Cèit 2026 · NCT07609394

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 10 agus nas sine · Fir · Air ùrachadh 22 Cèit 2026 · NCT06124196

Vasodilator and Exercise Study for DMD (VASO-REx)

A’ fastadhÌre 2
Aoisean 6 agus nas sine · Fir · Air ùrachadh 15 Cèit 2026 · NCT06290713

The Duchenne Registry

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 8 Cèit 2026 · NCT02069756

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 9 Gibl 2026 · NCT06839469

Urinary Titin Biomarker in DMD

A’ fastadhFàilte do shaor-thoilich fhallain
Aoisean 2 gu 10 · Fir · Air ùrachadh 8 Gibl 2026 · NCT07332013

Trial of Cell Based Therapy for DMD

A’ fastadhÌre 1
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 4 Màrt 2026 · NCT06692426

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

A’ fastadhÌre 1/2
Aoisean 4 gu 18 · Fir · Air ùrachadh 15 Dùbh 2025 · NCT04906460

Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy

A’ fastadhSgrùdadh amharc
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05016908

Biomarker Development for Muscular Dystrophies

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05019625

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim

A’ fastadhSgrùdadh amharc
Aoisean 10 agus nas sine · Fir · Air ùrachadh 6 Samh 2025 · NCT06093100

Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 gu 62 · Fir · Air ùrachadh 15 Dàmh 2025 · NCT01484678

DMD Voice: Qualitative Interviews With Patients and Caregivers

A’ fastadhSgrùdadh amharc
Aoisean 10 agus nas sine · Fir · Air ùrachadh 30 Gibl 2025 · NCT06925269

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.