Dachaigh › Dystrophy Fèithe Duchenne
Sgrùdaidhean clionaigeach Dystrophy Fèithe Duchenne a’ fastadh anns na SA
Tha 26 sgrùdaidhean airson Dystrophy Fèithe Duchenne a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.
Bailtean leis na sgrùdaidhean as motha
- Little Rock, AR7 sgrùdaidhean
- Chicago, IL5 sgrùdaidhean
- Durham, NC5 sgrùdaidhean
- Washington, DC5 sgrùdaidhean
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- Gainesville, FL5 sgrùdaidhean
- Boston, MA5 sgrùdaidhean
- Nashville, TN4 sgrùdaidhean
- Columbus, OH4 sgrùdaidhean
- Seattle, WA3 sgrùdaidhean
- Mountain View, CA3 sgrùdaidhean
- St. Louis, MO3 sgrùdaidhean
- Los Angeles, CA3 sgrùdaidhean
- Norfolk, VA3 sgrùdaidhean
- Cincinnati, OH3 sgrùdaidhean
- Portland, OR3 sgrùdaidhean
Le stàit
- Arkansas7 sgrùdaidhean
- California6 sgrùdaidhean
- Florida5 sgrùdaidhean
- Illinois5 sgrùdaidhean
- Massachusetts5 sgrùdaidhean
- Missouri3 sgrùdaidhean
- New York4 sgrùdaidhean
- North Carolina6 sgrùdaidhean
- Ohio5 sgrùdaidhean
- Oregon3 sgrùdaidhean
- Pennsylvania4 sgrùdaidhean
- Sgìre Cholumbia5 sgrùdaidhean
- Tennessee4 sgrùdaidhean
- Texas5 sgrùdaidhean
- Virginia4 sgrùdaidhean
- Washington3 sgrùdaidhean
Sgrùdaidhean air an ùrachadh o chionn ghoirid
Teacsa sgrùdaidh oifigeil (Beurla)
A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)
A’ fastadhÌre 3
Aoisean 7 gu 11 · Fir · Air ùrachadh 28 Sult 2026 · NCT07160634Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT
A’ fastadhSgrùdadh amharc
Aoisean 2 agus nas sine · Fir · Air ùrachadh 24 Sult 2026 · NCT06564974A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
A’ fastadhÌre 1
Aoisean 2 agus nas sine · Fir · Air ùrachadh 11 Sult 2026 · NCT04626674Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy
A’ fastadhÌre 1
Aoisean 8 gu 18 · Fir · Air ùrachadh 24 Lùna 2026 · NCT07172971The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Children With Duchenne Muscular Dystrophy
A’ fastadhSgrùdadh amharc
0 Days – 3 Years · Fir · Air ùrachadh 19 Lùna 2026 · NCT07092540Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients
A’ fastadh
Aoisean 6 agus nas sine · Fir · Air ùrachadh 17 Lùna 2026 · NCT07766980Once Weekly Infant Corticosteroid Trial for DMD
A’ fastadhÌre 4
1 Month – 30 Months · Fir · Air ùrachadh 14 Lùna 2026 · NCT05412394Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 28 Iuch 2026 · NCT07674758A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
A’ fastadhÌre 1/2
Aoisean 0 gu 17 · Fir · Air ùrachadh 8 Iuch 2026 · NCT06138639A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
A’ fastadhSgrùdadh amharc
Aoisean 6 agus nas sine · Gach gnè · Air ùrachadh 2 Iuch 2026 · NCT07127978PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)
A’ fastadhÌre 1/2
Aoisean 2 gu 7 · Fir · Air ùrachadh 23 Ògmh 2026 · NCT07429240Duchenne Electronic Health Record Study
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 27 Cèit 2026 · NCT07609394Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
A’ fastadhÌre 3
Aoisean 4 gu 18 · Fir · Air ùrachadh 27 Cèit 2026 · NCT07608432Wearable Technology to Evaluate Hyperglycemia and HRV in DMD
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 10 agus nas sine · Fir · Air ùrachadh 22 Cèit 2026 · NCT06124196Vasodilator and Exercise Study for DMD (VASO-REx)
A’ fastadhÌre 2
Aoisean 6 agus nas sine · Fir · Air ùrachadh 15 Cèit 2026 · NCT06290713The Duchenne Registry
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 8 Cèit 2026 · NCT02069756Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 9 Gibl 2026 · NCT06839469Urinary Titin Biomarker in DMD
A’ fastadhFàilte do shaor-thoilich fhallain
Aoisean 2 gu 10 · Fir · Air ùrachadh 8 Gibl 2026 · NCT07332013Trial of Cell Based Therapy for DMD
A’ fastadhÌre 1
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 4 Màrt 2026 · NCT06692426Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)
A’ fastadhÌre 1/2
Aoisean 4 gu 18 · Fir · Air ùrachadh 15 Dùbh 2025 · NCT04906460Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy
A’ fastadhSgrùdadh amharc
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05016908Biomarker Development for Muscular Dystrophies
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05019625Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim
A’ fastadhSgrùdadh amharc
Aoisean 10 agus nas sine · Fir · Air ùrachadh 6 Samh 2025 · NCT06093100Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 gu 62 · Fir · Air ùrachadh 15 Dàmh 2025 · NCT01484678DMD Voice: Qualitative Interviews With Patients and Caregivers
A’ fastadhSgrùdadh amharc
Aoisean 10 agus nas sine · Fir · Air ùrachadh 30 Gibl 2025 · NCT06925269Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.