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Dachaigh › Dystrophy Fèithe Duchenne › North Carolina

Sgrùdaidhean clionaigeach Dystrophy Fèithe Duchenne ann an North Carolina

Tha 6 sgrùdaidhean airson Dystrophy Fèithe Duchenne a’ lorg phàirtichean aig làraichean ann an North Carolina.

Bailtean ann an North Carolina

Teacsa sgrùdaidh oifigeil (Beurla)

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • Duke University Medical Center, Durham
A’ fastadhÌre 1
Aoisean 2 agus nas sine · Fir · Air ùrachadh 11 Sult 2026 · NCT04626674

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • Duke Children's Hospital, Durham
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 28 Iuch 2026 · NCT07674758

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

  • Duke University / Lenox Baker Children's Hospital, Durham
A’ fastadhSgrùdadh amharc
Aoisean 6 agus nas sine · Gach gnè · Air ùrachadh 2 Iuch 2026 · NCT07127978

Duchenne Electronic Health Record Study

  • Duke University Medical Center, Durham
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 27 Cèit 2026 · NCT07609394

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

  • Rare Disease Research, LLC, Hillsborough
A’ fastadhÌre 3
Aoisean 4 gu 18 · Fir · Air ùrachadh 27 Cèit 2026 · NCT07608432

Biomarker Development for Muscular Dystrophies

  • Wake Forest University, Winston-Salem
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05019625

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.