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Sgrùdaidhean clionaigeach Ataxia Friedreich ann an Pennsylvania

Tha 4 sgrùdaidhean airson Ataxia Friedreich a’ lorg phàirtichean aig làraichean ann an Pennsylvania.

Bailtean ann an Pennsylvania

Teacsa sgrùdaidh oifigeil (Beurla)

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
A’ fastadhÌre 1
Aoisean 18 gu 40 · Gach gnè · Air ùrachadh 29 Sult 2026 · NCT07180355

An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia

  • Children's Hospital of the University of Pennsylvania (CHOP), Philadelphia
A’ fastadhÌre 2
Aoisean 2 gu 60 · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT06447025

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • Children's Hospital of Philadelphia, Philadelphia
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 1 Sult 2026 · NCT06016946

A Study to Learn More About the Long-Term Safety of BIIB141 (Omaveloxolone) in Participants With Friedreich's Ataxia Who Are Prescribed it by Their Own Doctors

  • Children's Hospital of Philadelphia, Philadelphia
A’ fastadhSgrùdadh amharc
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 28 Gibl 2026 · NCT06623890

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.