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Sgrùdaidhean clionaigeach Galar Gaucher a’ fastadh anns na SA

Tha 14 sgrùdaidhean airson Galar Gaucher a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

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Teacsa sgrùdaidh oifigeil (Beurla)

Gaucher Disease Outcome Survey (GOS)

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 15 Sult 2026 · NCT03291223

A Long-term Follow-up Study of Gaucher Disease

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT03190837

A Gaucher Disease Gene Therapy Trial With FLT201

A’ fastadhÌre 3
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT07223944

Advancing Integrated Therapies for Gaucher Disease

A’ fastadhSgrùdadh amharc
3 Months – 75 Years · Gach gnè · Air ùrachadh 11 Lùna 2026 · NCT07758816

MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)

A’ fastadhSgrùdadh amharc
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 4 Lùna 2026 · NCT05586243

Oxidative Stress and Inflammatory Biomarkers in Gaucher Disease

A’ fastadhSgrùdadh amharc
Aoisean 18 gu 75 · Gach gnè · Air ùrachadh 13 Iuch 2026 · NCT02437396

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 14 Gibl 2026 · NCT00358943

Registry of Patients Diagnosed With Lysosomal Storage Diseases

A’ fastadhSgrùdadh amharc
Suas gu aois 64 · Gach gnè · Air ùrachadh 8 Gibl 2026 · NCT05619900

Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease

A’ fastadhSgrùdadh amharc
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 6 Gibl 2026 · NCT05843552

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

A’ fastadhÌre 1
Aoisean 18 gu 50 · Banairean · Air ùrachadh 17 Màrt 2026 · NCT04532047

Longitudinal Study of Neurodegenerative Disorders

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 9 Gearr 2026 · NCT03333200

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.