Dachaigh › Galar Gaucher
Sgrùdaidhean clionaigeach Galar Gaucher a’ fastadh anns na SA
Tha 14 sgrùdaidhean airson Galar Gaucher a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.
Bailtean leis na sgrùdaidhean as motha
- Minneapolis, MN5 sgrùdaidhean
- Pittsburgh, PA5 sgrùdaidhean
- San Francisco, CA4 sgrùdaidhean
- Durham, NC4 sgrùdaidhean
Le stàit
- California4 sgrùdaidhean
- Minnesota5 sgrùdaidhean
- North Carolina4 sgrùdaidhean
- Pennsylvania5 sgrùdaidhean
Sgrùdaidhean air an ùrachadh o chionn ghoirid
Teacsa sgrùdaidh oifigeil (Beurla)
Gaucher Disease Outcome Survey (GOS)
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 15 Sult 2026 · NCT03291223A Long-term Follow-up Study of Gaucher Disease
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT03190837A Gaucher Disease Gene Therapy Trial With FLT201
A’ fastadhÌre 3
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT07223944Advancing Integrated Therapies for Gaucher Disease
A’ fastadhSgrùdadh amharc
3 Months – 75 Years · Gach gnè · Air ùrachadh 11 Lùna 2026 · NCT07758816MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 4 Lùna 2026 · NCT05586243Oxidative Stress and Inflammatory Biomarkers in Gaucher Disease
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 75 · Gach gnè · Air ùrachadh 13 Iuch 2026 · NCT02437396International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 14 Gibl 2026 · NCT00358943Registry of Patients Diagnosed With Lysosomal Storage Diseases
A’ fastadhSgrùdadh amharc
Suas gu aois 64 · Gach gnè · Air ùrachadh 8 Gibl 2026 · NCT05619900Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 6 Gibl 2026 · NCT05843552Study of CAR T-Cells Targeting the GD2 With IL-15+iCaspase9 for Relapsed/Refractory Neuroblastoma or Relapsed/Refractory Osteosarcoma
A’ fastadhÌre 1
18 Months · Gach gnè · Air ùrachadh 27 Màrt 2026 · NCT03721068PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
A’ fastadhÌre 1
Aoisean 18 gu 50 · Banairean · Air ùrachadh 17 Màrt 2026 · NCT04532047Longitudinal Study of Neurodegenerative Disorders
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 9 Gearr 2026 · NCT03333200Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
A’ fastadhSgrùdadh amharc
2 Months – 60 Years · Gach gnè · Air ùrachadh 13 Faoi 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
A’ fastadhÌre 2
2 Months – 55 Years · Gach gnè · Air ùrachadh 15 Dùbh 2025 · NCT01962415Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.