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Sgrùdaidhean clionaigeach Galar Gaucher ann an California

Tha 4 sgrùdaidhean airson Galar Gaucher a’ lorg phàirtichean aig làraichean ann an California.

Bailtean ann an California

Teacsa sgrùdaidh oifigeil (Beurla)

A Gaucher Disease Gene Therapy Trial With FLT201

  • Kaiser Permanente - CA, Los Angeles
  • UCLA Health, Los Angeles
  • University of California, San Francisco (UCSF), San Francisco
A’ fastadhÌre 3
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT07223944

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  • Tower Hematology Oncology Medical Group- Site Number : 840056, Beverly Hills
  • University of California at Irvine- Site Number : 840036, Irvine
  • Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
  • agus 4 a bharrachd
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 14 Gibl 2026 · NCT00358943

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
A’ fastadhSgrùdadh amharc
Suas gu aois 64 · Gach gnè · Air ùrachadh 8 Gibl 2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

  • University of California, San Francisco
A’ fastadhÌre 1
Aoisean 18 gu 50 · Banairean · Air ùrachadh 17 Màrt 2026 · NCT04532047

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.