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Sgrùdaidhean clionaigeach Galairean Ginteil ann an California

Tha 16 sgrùdaidhean airson Galairean Ginteil a’ lorg phàirtichean aig làraichean ann an California.

Bailtean ann an California

Teacsa sgrùdaidh oifigeil (Beurla)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of California, Los Angeles, Los Angeles
  • University of California, Irvine Medical Center, Orange
  • Stanford University, Stanford
  • agus 2 a bharrachd
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 100 Years · Gach gnè · Air ùrachadh 2 Dàmh 2026 · NCT02450851

Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia

  • UCSF Benioff Children's Hospital Oakland, Oakland
A’ fastadhÌre 2/3
Aoisean 2 gu 17 · Gach gnè · Air ùrachadh 24 Sult 2026 · NCT07441876

A Long-Term Observational Study of Patients With Fucosidosis

  • Children's Hospital of Orange County, Orange
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 17 Sult 2026 · NCT07615400

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • UCLA Ataxia Center, Los Angeles
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 1 Sult 2026 · NCT06016946

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • University of California Irvine, Orange
A’ fastadhÌre 2
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 5 Lùna 2026 · NCT07224360

Prospective Clinical Assessment Study in Children With Hypochondroplasia

  • UCSF Benioff Children's Hospital, Oakland
A’ fastadhSgrùdadh amharc
30 Months – 16 Years · Gach gnè · Air ùrachadh 16 Iuch 2026 · NCT06410976

Rett Syndrome Registry

  • Children's Hospital Los Angeles, Los Angeles
  • UCSF Benioff Children's Hospital, Oakland
  • Rady Children's Hospital - San Diego, San Diego
A’ fastadhSgrùdadh amharc
Aoisean 0 gu 99 · Gach gnè · Air ùrachadh 30 Ògmh 2026 · NCT05432349

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • Ronald Reagan UCLA Medical Center, Los Angeles
  • University of Stanford Medical Center, Palo Alto
A’ fastadhÌre 1/2
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 23 Màrt 2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • UCSD Altman Clinical and Transalational Research Institute Building, Los Angeles
  • Ronald Reagan UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital Stanford, Stanford
A’ fastadhÌre 1/2
Gach aois · Gach gnè · Air ùrachadh 22 Faoi 2026 · NCT04159103

An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705

  • UCLA Medical Center, Los Angeles
  • Lucile Packard Children's Hospital at Stanford, Palo Alto
  • Altman Clinical and Translational Research Institution, San Diego
A’ fastadhÌre 1/2
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 23 Dùbh 2025 · NCT05295433

STXBP1 and SYNGAP1 Related Disorders Natural History Study

  • Stanford Medicine Children's Health, Palo Alto
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 29 Dàmh 2025 · NCT06555965

Large Language Models To Improve the Quality of Care of Cardiology Patients

  • Stanford, Palo Alto
A’ fastadh
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 15 Cèit 2025 · NCT06935253

Natural History Study of Patients with HPDL Mutations

  • Eun Hae Lee, San Diego
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 30 Màrt 2025 · NCT05848271

An Adaptive Clinical Trial of BeginNGS Newborn Screening for Hundreds of Genetic Diseases by Genome Sequencing

  • Rady Children's Hospital San Diego, San Diego
A’ fastadhFàilte do shaor-thoilich fhallain
1 Day – 28 Days · Gach gnè · Air ùrachadh 12 Màrt 2024 · NCT06306521

Rady Children's Institute Genomic Biorepository

  • Rady Pediatric Genomics & Systems Medicine Institute, San Diego
A’ fastadhFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 12 Dùbh 2022 · NCT02917460

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.