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Sgrùdaidhean clionaigeach Galairean Ginteil ann an Florida
Tha 7 sgrùdaidhean airson Galairean Ginteil a’ lorg phàirtichean aig làraichean ann an Florida.
Bailtean ann an Florida
Teacsa sgrùdaidh oifigeil (Beurla)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Miami Miller School of Medicine, Miami
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 100 Years · Gach gnè · Air ùrachadh 2 Dàmh 2026 · NCT02450851Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- University of Florida - Neurology, Gainesville
- USF Ataxia Research Center, Tampa
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 1 Sult 2026 · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 103, Gainesville
- GC2501 Study Site 105, Miami
A’ fastadhÌre 3
Aoisean 18 gu 80 · Gach gnè · Air ùrachadh 11 Lùna 2026 · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- The Foundation for Sickle Cell Disease, Hollywood
A’ fastadhÌre 2
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 5 Lùna 2026 · NCT07224360Rett Syndrome Registry
- Nicklaus Children's Hospital, Miami
A’ fastadhSgrùdadh amharc
Aoisean 0 gu 99 · Gach gnè · Air ùrachadh 30 Ògmh 2026 · NCT05432349A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)
- Sirven and Associates, Miami
A’ fastadhSgrùdadh amharc
Aoisean 12 agus nas sine · Gach gnè · Air ùrachadh 3 Ògmh 2026 · NCT07001280Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Nicklaus Children's Hospital, Miami
- University of South Florida - 12901 Bruce B Downs, Tampa
A’ fastadhÌre 1/2
Gach aois · Gach gnè · Air ùrachadh 22 Faoi 2026 · NCT04159103Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.