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Sgrùdaidhean clionaigeach Mearachdan Metabolism Co-roinnte a’ fastadh anns na SA
Tha 11 sgrùdaidhean airson Mearachdan Metabolism Co-roinnte a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.
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Le stàit
Sgrùdaidhean air an ùrachadh o chionn ghoirid
Teacsa sgrùdaidh oifigeil (Beurla)
Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 100 Years · Gach gnè · Air ùrachadh 28 Sult 2026 · NCT02890342A Long-Term Observational Study of Patients With Fucosidosis
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 17 Sult 2026 · NCT07615400Clinical and Laboratory Study of Methylmalonic Acidemia
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 115 Years · Gach gnè · Air ùrachadh 10 Sult 2026 · NCT00078078Study of Alkaptonuria
A’ fastadhSgrùdadh amharc
Aoisean 2 gu 115 · Gach gnè · Air ùrachadh 1 Sult 2026 · NCT00005909Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
A’ fastadhSgrùdadh amharc
7 Months – 15 Months · Gach gnè · Air ùrachadh 31 Lùna 2026 · NCT06805695Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT
A’ fastadhÌre 1/2
1 Month – 25 Years · Gach gnè · Air ùrachadh 15 Gibl 2026 · NCT06839456Registry of Patients Diagnosed With Lysosomal Storage Diseases
A’ fastadhSgrùdadh amharc
Suas gu aois 64 · Gach gnè · Air ùrachadh 8 Gibl 2026 · NCT05619900A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study
A’ fastadhÌre 1/2
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 23 Màrt 2026 · NCT05130437Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC
A’ fastadhÌre 1 tràth
Suas gu aois 30 · Gach gnè · Air ùrachadh 20 Gearr 2026 · NCT02356653Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
A’ fastadhÌre 1/2
Gach aois · Gach gnè · Air ùrachadh 22 Faoi 2026 · NCT04159103An Extension Study to Evaluate the Long-Term Safety and Clinical Activity of mRNA-3705 in Participants Previously Enrolled in Other Clinical Studies of mRNA-3705
A’ fastadhÌre 1/2
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 23 Dùbh 2025 · NCT05295433Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.