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Dachaigh › Mearachdan Metabolism Co-roinnte › Pennsylvania

Sgrùdaidhean clionaigeach Mearachdan Metabolism Co-roinnte ann an Pennsylvania

Tha 6 sgrùdaidhean airson Mearachdan Metabolism Co-roinnte a’ lorg phàirtichean aig làraichean ann an Pennsylvania.

Bailtean ann an Pennsylvania

Teacsa sgrùdaidh oifigeil (Beurla)

Natural History, Physiology, Microbiome and Biochemistry Studies of Propionic Acidemia

  • Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 100 Years · Gach gnè · Air ùrachadh 28 Sult 2026 · NCT02890342

Clinical and Laboratory Study of Methylmalonic Acidemia

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
1 Month – 115 Years · Gach gnè · Air ùrachadh 10 Sult 2026 · NCT00078078

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

  • Children's Hospital of Philadelphia, Philadelphia
A’ fastadhÌre 1/2
1 Month – 25 Years · Gach gnè · Air ùrachadh 15 Gibl 2026 · NCT06839456

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
A’ fastadhÌre 1/2
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 23 Màrt 2026 · NCT05130437

Expanded Access Protocol Using CD3+/CD19+ Depleted PBSC

  • Children's Hospital of Philadelphia, Philadelphia
A’ fastadhÌre 1 tràth
Suas gu aois 30 · Gach gnè · Air ùrachadh 20 Gearr 2026 · NCT02356653

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Children's Hospital of Philadelphia (CHOP), Philadelphia
A’ fastadhÌre 1/2
Gach aois · Gach gnè · Air ùrachadh 22 Faoi 2026 · NCT04159103

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.