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Sgrùdaidhean clionaigeach Leukoencephalopathies ann an California
Tha 4 sgrùdaidhean airson Leukoencephalopathies a’ lorg phàirtichean aig làraichean ann an California.
Bailtean ann an California
Teacsa sgrùdaidh oifigeil (Beurla)
A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)
- UCSF Benioff Children's Hospital Oakland, Oakland
A’ fastadhÌre 1/2
30 Months · Gach gnè · Air ùrachadh 17 Gibl 2026 · NCT04998396North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)
- University of California San Diego, San Diego
- Lucile Packard Children's Hospital, Stanford
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 4 Gearr 2026 · NCT01694940The Myelin Disorders Biorepository Project
- Children's Hospital of Los Angeles, Los Angeles
- Children's Hospital of Orange County, Orange
- Stanford University (Lucile Packard Children's Hospital), Palo Alto
- agus 3 a bharrachd
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369Natural History Study of Patients with HPDL Mutations
- Eun Hae Lee, San Diego
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 30 Màrt 2025 · NCT05848271Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.