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Dachaigh › Leukoencephalopathies › California

Sgrùdaidhean clionaigeach Leukoencephalopathies ann an California

Tha 4 sgrùdaidhean airson Leukoencephalopathies a’ lorg phàirtichean aig làraichean ann an California.

Bailtean ann an California

Teacsa sgrùdaidh oifigeil (Beurla)

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • UCSF Benioff Children's Hospital Oakland, Oakland
A’ fastadhÌre 1/2
30 Months · Gach gnè · Air ùrachadh 17 Gibl 2026 · NCT04998396

North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

  • University of California San Diego, San Diego
  • Lucile Packard Children's Hospital, Stanford
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 4 Gearr 2026 · NCT01694940

The Myelin Disorders Biorepository Project

  • Children's Hospital of Los Angeles, Los Angeles
  • Children's Hospital of Orange County, Orange
  • Stanford University (Lucile Packard Children's Hospital), Palo Alto
  • agus 3 a bharrachd
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369

Natural History Study of Patients with HPDL Mutations

  • Eun Hae Lee, San Diego
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 30 Màrt 2025 · NCT05848271

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.