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Dachaigh › Leukoencephalopathies › Massachusetts

Sgrùdaidhean clionaigeach Leukoencephalopathies ann an Massachusetts

Tha 4 sgrùdaidhean airson Leukoencephalopathies a’ lorg phàirtichean aig làraichean ann an Massachusetts.

Bailtean ann an Massachusetts

Teacsa sgrùdaidh oifigeil (Beurla)

An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease

  • Massachusetts General Hospital /ID# 270960, Boston
A’ fastadhÌre 1/2
6 Months · Gach gnè · Air ùrachadh 24 Sult 2026 · NCT05757141

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • Massachusetts General Hospital (MGH); Center for Rare Neurological Diseases (CRND), Boston
A’ fastadhÌre 1/2
30 Months · Gach gnè · Air ùrachadh 17 Gibl 2026 · NCT04998396

North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)

  • Massachusetts General Hospital, Boston
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 4 Gearr 2026 · NCT01694940

The Myelin Disorders Biorepository Project

  • Massachusetts General Hospital (MGH), Boston
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.