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Sgrùdaidhean clionaigeach Dystrophy Myotonic ann an California

Tha 5 sgrùdaidhean airson Dystrophy Myotonic a’ lorg phàirtichean aig làraichean ann an California.

Bailtean ann an California

Teacsa sgrùdaidh oifigeil (Beurla)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • UCSD - Altman Clinical and Translational Research Institute, La Jolla
  • UCLA Medical Center (Department of Neurology), Los Angeles
  • Stanford Neuroscience Health Center, Palo Alto
A’ fastadhÌre 3
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 5 Dàmh 2026 · NCT07486934

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • University of California, San Diego, La Jolla
  • University of California, Los Angeles, Los Angeles
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT03981575

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

  • University of California, Los Angeles, Los Angeles
A’ fastadhSgrùdadh amharc
59 Months · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT05224778

Study of ATX-01 in Participants With DM1

  • UCLA, Los Angeles
A’ fastadhÌre 1/2
Aoisean 18 gu 64 · Gach gnè · Air ùrachadh 10 Gearr 2026 · NCT06300307

Myotonic Dystrophy Family Registry

  • Myotonic Dystrophy Foundation, Oakland
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 21 Samh 2024 · NCT02398786

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.