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Sgrùdaidhean clionaigeach Dystrophy Myotonic a’ fastadh anns na SA

Tha 19 sgrùdaidhean airson Dystrophy Myotonic a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

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Teacsa sgrùdaidh oifigeil (Beurla)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

A’ fastadhÌre 3
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 5 Dàmh 2026 · NCT07486934

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 4 Sult 2026 · NCT07700225

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

A’ fastadhSgrùdadh amharc
Aoisean 3 gu 17 · Gach gnè · Air ùrachadh 11 Lùna 2026 · NCT06747884

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT03981575

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

A’ fastadhSgrùdadh amharc
59 Months · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT05224778

Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy

A’ fastadhSgrùdadh amharc
Aoisean 0 gu 17 · Gach gnè · Air ùrachadh 5 Ògmh 2026 · NCT07630389

Investigating Exercise in Myotonic Dystrophy Type 2 (DM2)

A’ fastadh
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 15 Gibl 2026 · NCT06716931

Remote Assessments and Genetic Determinants of Myotonic Dystrophy

A’ fastadhSgrùdadh amharc
Aoisean 18 gu 88 · Gach gnè · Air ùrachadh 1 Gibl 2026 · NCT07505342

Study of ATX-01 in Participants With DM1

A’ fastadhÌre 1/2
Aoisean 18 gu 64 · Gach gnè · Air ùrachadh 10 Gearr 2026 · NCT06300307

Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 23 Faoi 2026 · NCT07362875

Extracellular RNA Biomarkers of Myotonic Dystrophy

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05020002

Biomarker Development for Muscular Dystrophies

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05019625

Cerebrospinal Fluid Biomarkers of Myotonic Dystrophy

A’ fastadhSgrùdadh amharc
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT06075693

Long-Term Development of Muscular Dystrophy Outcome Assessments

A’ fastadhSgrùdadh amharc
Aoisean 6 gu 50 · Gach gnè · Air ùrachadh 18 Samh 2025 · NCT05989620

Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry

A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 15 Dàmh 2025 · NCT00082108

Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy

A’ fastadhÌre 2/3
Aoisean 6 gu 45 · Gach gnè · Air ùrachadh 28 Cèit 2025 · NCT05004129

Myotonic Dystrophy Family Registry

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 21 Samh 2024 · NCT02398786

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.