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Sgrùdaidhean clionaigeach Dystrophy Myotonic a’ fastadh anns na SA
Tha 19 sgrùdaidhean airson Dystrophy Myotonic a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.
Bailtean leis na sgrùdaidhean as motha
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- Boston, MA4 sgrùdaidhean
- Gainesville, FL4 sgrùdaidhean
- Los Angeles, CA4 sgrùdaidhean
- Cedar Rapids, IA3 sgrùdaidhean
Le stàit
- California5 sgrùdaidhean
- Florida4 sgrùdaidhean
- Iowa3 sgrùdaidhean
- Kansas4 sgrùdaidhean
- Massachusetts4 sgrùdaidhean
- New York8 sgrùdaidhean
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- Pennsylvania3 sgrùdaidhean
- Texas3 sgrùdaidhean
- Virginia8 sgrùdaidhean
Sgrùdaidhean air an ùrachadh o chionn ghoirid
Teacsa sgrùdaidh oifigeil (Beurla)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
A’ fastadhÌre 3
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 5 Dàmh 2026 · NCT07486934A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1
A’ fastadhÌre 1/2
Aoisean 10 gu 55 · Gach gnè · Air ùrachadh 21 Sult 2026 · NCT06844214Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 4 Sult 2026 · NCT07700225Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension
A’ fastadhSgrùdadh amharc
Aoisean 3 gu 17 · Gach gnè · Air ùrachadh 11 Lùna 2026 · NCT06747884Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT03981575DMCRN-02-001: Assessing Pediatric Endpoints in DM1
A’ fastadhSgrùdadh amharc
59 Months · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT05224778Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy
A’ fastadhSgrùdadh amharc
Aoisean 0 gu 17 · Gach gnè · Air ùrachadh 5 Ògmh 2026 · NCT07630389Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
A’ fastadhÌre 3
Aoisean 4 gu 18 · Fir · Air ùrachadh 27 Cèit 2026 · NCT07608432Investigating Exercise in Myotonic Dystrophy Type 2 (DM2)
A’ fastadh
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 15 Gibl 2026 · NCT06716931Remote Assessments and Genetic Determinants of Myotonic Dystrophy
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 88 · Gach gnè · Air ùrachadh 1 Gibl 2026 · NCT07505342Study of ATX-01 in Participants With DM1
A’ fastadhÌre 1/2
Aoisean 18 gu 64 · Gach gnè · Air ùrachadh 10 Gearr 2026 · NCT06300307Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 23 Faoi 2026 · NCT07362875Extracellular RNA Biomarkers of Myotonic Dystrophy
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05020002Biomarker Development for Muscular Dystrophies
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05019625Cerebrospinal Fluid Biomarkers of Myotonic Dystrophy
A’ fastadhSgrùdadh amharc
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT06075693Long-Term Development of Muscular Dystrophy Outcome Assessments
A’ fastadhSgrùdadh amharc
Aoisean 6 gu 50 · Gach gnè · Air ùrachadh 18 Samh 2025 · NCT05989620Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Gach aois · Gach gnè · Air ùrachadh 15 Dàmh 2025 · NCT00082108Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
A’ fastadhÌre 2/3
Aoisean 6 gu 45 · Gach gnè · Air ùrachadh 28 Cèit 2025 · NCT05004129Myotonic Dystrophy Family Registry
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 21 Samh 2024 · NCT02398786Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.