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Sgrùdaidhean clionaigeach Dystrophy Myotonic ann an Florida

Tha 4 sgrùdaidhean airson Dystrophy Myotonic a’ lorg phàirtichean aig làraichean ann an Florida.

Bailtean ann an Florida

Teacsa sgrùdaidh oifigeil (Beurla)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • UF Health: University of Florida Clinical Research Center, Gainesville
A’ fastadhÌre 3
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 5 Dàmh 2026 · NCT07486934

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

  • University of Florida, 2004 Mowry Road - Site Number: 8400005, Gainesville
  • University of South Florida - Neuromuscular Research, 13330 USF Laurel Drive - Site Number: 8400001, Tampa
A’ fastadhÌre 1/2
Aoisean 10 gu 55 · Gach gnè · Air ùrachadh 21 Sult 2026 · NCT06844214

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • University of Florida, Gainesville
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT03981575

Study of ATX-01 in Participants With DM1

  • University of Florida, Gainesville
A’ fastadhÌre 1/2
Aoisean 18 gu 64 · Gach gnè · Air ùrachadh 10 Gearr 2026 · NCT06300307

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.