Dachaigh › Dystrophy Myotonic › North Carolina
Sgrùdaidhean clionaigeach Dystrophy Myotonic ann an North Carolina
Tha 4 sgrùdaidhean airson Dystrophy Myotonic a’ lorg phàirtichean aig làraichean ann an North Carolina.
Teacsa sgrùdaidh oifigeil (Beurla)
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1
- Rare Disease Research, LLC, Hillsborough
A’ fastadhÌre 3
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 5 Dàmh 2026 · NCT07486934Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
- Rare Disease Research, LLC, Hillsborough
A’ fastadhÌre 3
Aoisean 4 gu 18 · Fir · Air ùrachadh 27 Cèit 2026 · NCT07608432Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy
- Wake Forest University Health Sciences, Winston-Salem
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 23 Faoi 2026 · NCT07362875Biomarker Development for Muscular Dystrophies
- Wake Forest University, Winston-Salem
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05019625Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.