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Sgrùdaidhean clionaigeach Dystrophy Myotonic ann an North Carolina

Tha 4 sgrùdaidhean airson Dystrophy Myotonic a’ lorg phàirtichean aig làraichean ann an North Carolina.

Teacsa sgrùdaidh oifigeil (Beurla)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • Rare Disease Research, LLC, Hillsborough
A’ fastadhÌre 3
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 5 Dàmh 2026 · NCT07486934

Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

  • Rare Disease Research, LLC, Hillsborough
A’ fastadhÌre 3
Aoisean 4 gu 18 · Fir · Air ùrachadh 27 Cèit 2026 · NCT07608432

Development of Quantitative Muscle Imaging as a Biomarker of Disease Endpoints in Myotonic Dystrophy

  • Wake Forest University Health Sciences, Winston-Salem
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 23 Faoi 2026 · NCT07362875

Biomarker Development for Muscular Dystrophies

  • Wake Forest University, Winston-Salem
A’ fastadhSgrùdadh amharcFàilte do shaor-thoilich fhallain
Aoisean 5 agus nas sine · Gach gnè · Air ùrachadh 24 Samh 2025 · NCT05019625

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.