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Sgrùdaidhean clionaigeach Dystrophy Myotonic ann an Virginia

Tha 8 sgrùdaidhean airson Dystrophy Myotonic a’ lorg phàirtichean aig làraichean ann an Virginia.

Bailtean ann an Virginia

Teacsa sgrùdaidh oifigeil (Beurla)

Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1

  • Virginia Commonwealth University - Biotech One, Richmond
A’ fastadhÌre 3
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 5 Dàmh 2026 · NCT07486934

A Study to Investigate the Safety, Tolerability, and Efficacy of SAR446268, an Adeno-associated Viral Vector-mediated Gene Therapy in Participants Aged 10 to 55 Years of Age With Non-congenital Myotonic Dystrophy Type 1

  • Virginia Commonwealth University Medical Center- Site Number : 8400006, Richmond
A’ fastadhÌre 1/2
Aoisean 10 gu 55 · Gach gnè · Air ùrachadh 21 Sult 2026 · NCT06844214

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

  • Virginia Commonwealth University, Richmond
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 4 Sult 2026 · NCT07700225

Trial Readiness and Endpoint Assessment in Pediatric Myotonic Dystrophy Extension

  • Virginia Commonwealth University, Richmond
A’ fastadhSgrùdadh amharc
Aoisean 3 gu 17 · Gach gnè · Air ùrachadh 11 Lùna 2026 · NCT06747884

Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1)

  • Virginia Commonwealth University, Richmond
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 70 · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT03981575

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

  • Virginia Commonwealth University, Richmond
A’ fastadhSgrùdadh amharc
59 Months · Gach gnè · Air ùrachadh 10 Ògmh 2026 · NCT05224778

Study of ATX-01 in Participants With DM1

  • Virginia Commonwealth University, Richmond
A’ fastadhÌre 1/2
Aoisean 18 gu 64 · Gach gnè · Air ùrachadh 10 Gearr 2026 · NCT06300307

Long-Term Development of Muscular Dystrophy Outcome Assessments

  • Virginia Commonwealth University, Richmond
A’ fastadhSgrùdadh amharc
Aoisean 6 gu 50 · Gach gnè · Air ùrachadh 18 Samh 2025 · NCT05989620

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.