Dachaigh › Galar Pelizaeus-Merzbacher
Sgrùdaidhean clionaigeach Galar Pelizaeus-Merzbacher a’ fastadh anns na SA
Tha 5 sgrùdaidhean airson Galar Pelizaeus-Merzbacher a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.
Bailtean leis na sgrùdaidhean as motha
Le stàit
Sgrùdaidhean air an ùrachadh o chionn ghoirid
Teacsa sgrùdaidh oifigeil (Beurla)
Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease
A’ fastadhSgrùdadh amharc
6 Months – 17 Years · Fir · Air ùrachadh 2 Dàmh 2026 · NCT05659901UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
A’ fastadhÌre 1
1 Week – 22 Years · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT02254863Longitudinal Study of Neurodegenerative Disorders
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 9 Gearr 2026 · NCT03333200Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
A’ fastadhÌre 1
Aoisean 2 gu 17 · Fir · Air ùrachadh 12 Dùbh 2025 · NCT06150716The Myelin Disorders Biorepository Project
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.