Dachaigh › Galar Pelizaeus-Merzbacher › Pennsylvania
Sgrùdaidhean clionaigeach Galar Pelizaeus-Merzbacher ann an Pennsylvania
Tha 4 sgrùdaidhean airson Galar Pelizaeus-Merzbacher a’ lorg phàirtichean aig làraichean ann an Pennsylvania.
Bailtean ann an Pennsylvania
Teacsa sgrùdaidh oifigeil (Beurla)
Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease
- Ionis Investigative Site, Philadelphia
A’ fastadhSgrùdadh amharc
6 Months – 17 Years · Fir · Air ùrachadh 2 Dàmh 2026 · NCT05659901Longitudinal Study of Neurodegenerative Disorders
- UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 9 Gearr 2026 · NCT03333200Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)
- Ionis Investigative Site, Philadelphia
A’ fastadhÌre 1
Aoisean 2 gu 17 · Fir · Air ùrachadh 12 Dùbh 2025 · NCT06150716The Myelin Disorders Biorepository Project
- The Children's Hospital of Philadelphia, Philadelphia
- University of Pennsylvania, Philadelphia
- University of Pittsburgh Medical Center, Pittsburgh
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.