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Dachaigh › Galar Pelizaeus-Merzbacher › Pennsylvania

Sgrùdaidhean clionaigeach Galar Pelizaeus-Merzbacher ann an Pennsylvania

Tha 4 sgrùdaidhean airson Galar Pelizaeus-Merzbacher a’ lorg phàirtichean aig làraichean ann an Pennsylvania.

Bailtean ann an Pennsylvania

Teacsa sgrùdaidh oifigeil (Beurla)

Rocket Study: A Study to Characterize Biomarkers and Disease Progression in Participants With Pelizaeus-Merzbacher Disease

  • Ionis Investigative Site, Philadelphia
A’ fastadhSgrùdadh amharc
6 Months – 17 Years · Fir · Air ùrachadh 2 Dàmh 2026 · NCT05659901

Longitudinal Study of Neurodegenerative Disorders

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 9 Gearr 2026 · NCT03333200

Orbit Study: A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of Intrathecally Administered ION356 in Participants With Pelizaeus Merzbacher Disease (PMD)

  • Ionis Investigative Site, Philadelphia
A’ fastadhÌre 1
Aoisean 2 gu 17 · Fir · Air ùrachadh 12 Dùbh 2025 · NCT06150716

The Myelin Disorders Biorepository Project

  • The Children's Hospital of Philadelphia, Philadelphia
  • University of Pennsylvania, Philadelphia
  • University of Pittsburgh Medical Center, Pittsburgh
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 23 Dàmh 2025 · NCT03047369

Bho ClinicalTrials.gov, dàta air a thogail 6 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.