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Dachaigh › Phenylketonuria

Sgrùdaidhean clionaigeach Phenylketonuria a’ fastadh anns na SA

Tha 14 sgrùdaidhean airson Phenylketonuria a’ fastadh phàirtichean aig làraichean air feadh nan Stàitean Aonaichte.

Bailtean leis na sgrùdaidhean as motha

Le stàit

Sgrùdaidhean air an ùrachadh o chionn ghoirid

Teacsa sgrùdaidh oifigeil (Beurla)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

A’ fastadhÌre 1
Aoisean 18 gu 69 · Gach gnè · Air ùrachadh 28 Sult 2026 · NCT07241234

A Study of Sepiapterin in Participants With Phenylketonuria (PKU)

A’ fastadhÌre 3
Suas gu aois 9 · Gach gnè · Air ùrachadh 28 Lùna 2026 · NCT06302348

PheCheck™ Validation Study

A’ fastadhSgrùdadh amharc
Aoisean 1 agus nas sine · Gach gnè · Air ùrachadh 25 Lùna 2026 · NCT07551921

A Study of MZE782 in Adults With PKU

A’ fastadhÌre 2
Aoisean 18 gu 75 · Gach gnè · Air ùrachadh 20 Lùna 2026 · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

A’ fastadhÌre 1/2
Aoisean 18 gu 55 · Gach gnè · Air ùrachadh 18 Lùna 2026 · NCT06332807

A Trial to Examine if Repinatrabit is Processed Differently in Adults With Reduced Liver or Kidney Function Compared to Adults With Normal Liver and Kidney Function

A’ fastadhÌre 1Fàilte do shaor-thoilich fhallain
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 12 Lùna 2026 · NCT07713758

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

A’ fastadhÌre 3
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 8 Iuch 2026 · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

A’ fastadhÌre 4
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 17 Ògmh 2026 · NCT07477691

Educational, Social Support, and Nutritional Interventions and Their Cumulative Effect on Pregnancy Outcomes and Quality of Life in Teen and Adult Women With Phenylketonuria

A’ fastadhFàilte do shaor-thoilich fhallain
Aoisean 11 agus nas sine · Banairean · Air ùrachadh 7 Cèit 2026 · NCT01659749

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

A’ fastadhÌre 3
Aoisean 4 agus nas sine · Gach gnè · Air ùrachadh 1 Cèit 2026 · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 25 Màrt 2026 · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 24 Màrt 2026 · NCT06305234

Nutritional Impacts of Palynziq on Patients With Phenylketonuria (PKU)

A’ fastadhSgrùdadh amharc
Aoisean 16 agus nas sine · Gach gnè · Air ùrachadh 14 Faoi 2026 · NCT04404530

Development of Novel Psychological Assessment Tools and Anxiety Intervention for Phenylketonuria

A’ fastadh
Aoisean 10 gu 17 · Gach gnè · Air ùrachadh 23 Dùbh 2025 · NCT06560736

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.