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Dachaigh › Phenylketonuria › Pennsylvania

Sgrùdaidhean clionaigeach Phenylketonuria ann an Pennsylvania

Tha 8 sgrùdaidhean airson Phenylketonuria a’ lorg phàirtichean aig làraichean ann an Pennsylvania.

Bailtean ann an Pennsylvania

Teacsa sgrùdaidh oifigeil (Beurla)

A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria

  • UPMC Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhÌre 1
Aoisean 18 gu 69 · Gach gnè · Air ùrachadh 28 Sult 2026 · NCT07241234

A Study of MZE782 in Adults With PKU

  • Clinic for Special Children, Gordonville
A’ fastadhÌre 2
Aoisean 18 gu 75 · Gach gnè · Air ùrachadh 20 Lùna 2026 · NCT07694440

AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom)

  • University of Pittsburgh Medical Center, Pittsburgh
A’ fastadhÌre 1/2
Aoisean 18 gu 55 · Gach gnè · Air ùrachadh 18 Lùna 2026 · NCT06332807

A Study of JNT-517 in Participants With Phenylketonuria (PKU)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhÌre 3
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 8 Iuch 2026 · NCT06971731

Immune Modulation During Palynziq® Treatment in Adults (IMPALA)

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Philadelphia
A’ fastadhÌre 4
Aoisean 18 gu 65 · Gach gnè · Air ùrachadh 17 Ògmh 2026 · NCT07477691

A Long-Term Study of JNT-517 in Participants With Phenylketonuria

  • University of Pittsburgh Medical Center (UPMC) - Children's Hospital of Pittsburgh, Pittsburgh
A’ fastadhÌre 3
Aoisean 4 agus nas sine · Gach gnè · Air ùrachadh 1 Cèit 2026 · NCT06628128

A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)

  • University of Pittsburgh Medical Center, Pittsburgh
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 25 Màrt 2026 · NCT05813678

A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)

  • University of Pittsburgh Medical Center, Pittsburgh
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 24 Màrt 2026 · NCT06305234

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.