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Sgrùdaidhean clionaigeach Atrophy Fèitheach an Droma ann an Florida

Tha 8 sgrùdaidhean airson Atrophy Fèitheach an Droma a’ lorg phàirtichean aig làraichean ann an Florida.

Bailtean ann an Florida

Teacsa sgrùdaidh oifigeil (Beurla)

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy

  • University of Florida Pediatrics, Gainesville
A’ fastadhÌre 4
3 Months – 24 Months · Gach gnè · Air ùrachadh 2 Dàmh 2026 · NCT05861986

A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy

  • University of Florida Pediatrics, Gainesville
A’ fastadhÌre 4
3 Months – 24 Months · Gach gnè · Air ùrachadh 10 Sult 2026 · NCT05861999

A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)

  • Nemours Children's Hospital, Orlando, Orlando
A’ fastadhÌre 1
Aoisean 3 agus nas sine · Gach gnè · Air ùrachadh 3 Sult 2026 · NCT06555419

Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy

  • Nemours Children's Hospital, Florida, Orlando
A’ fastadh
Aoisean 3 agus nas sine · Gach gnè · Air ùrachadh 19 Lùna 2026 · NCT05866419

Clinical Procedures to Support Research in ALS

  • University of Miami, Miami
A’ fastadhSgrùdadh amharc
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 15 Ògmh 2026 · NCT03489278

ALS/MND Natural History Study Data Repository

  • University of Florida, Gainesville
A’ fastadhSgrùdadh amharc
Aoisean 18 gu 90 · Gach gnè · Air ùrachadh 20 Cèit 2026 · NCT05966038

Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)

  • Golisano Children's Hospital of Southwest Florida, Fort Myers
  • Jackson South Medical Center, Palmetto Bay
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 31 Faoi 2025 · NCT04174157

Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.