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Sgrùdaidhean clionaigeach Atrophy Fèitheach an Droma ann an North Carolina
Tha 3 sgrùdaidhean airson Atrophy Fèitheach an Droma a’ lorg phàirtichean aig làraichean ann an North Carolina.
Bailtean ann an North Carolina
Teacsa sgrùdaidh oifigeil (Beurla)
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Rare Disease Research NC, LLC, Hillsborough
A’ fastadhÌre 2
Aoisean 5 gu 17 · Gach gnè · Air ùrachadh 14 Sult 2026 · NCT07287982Clinical Procedures to Support Research in ALS
- Duke University, Durham
- Wake Forest University, Winston-Salem
A’ fastadhSgrùdadh amharc
Aoisean 18 agus nas sine · Gach gnè · Air ùrachadh 15 Ògmh 2026 · NCT03489278Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Duke Health, Durham
A’ fastadhSgrùdadh amharc
Gach aois · Gach gnè · Air ùrachadh 31 Faoi 2025 · NCT04174157Bho ClinicalTrials.gov, dàta air a thogail 5 Dàmh 2026. Bidh gach sgrùdadh a’ suidheachadh a chuidi fhèin; bidh an sgioba sgrùdaidh a’ co-dhùnadh cò as urrainn pàirt a ghabhail.