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Kliničke studije za Genetski poremećaji u državi Florida

7 studija za Genetski poremećaji traži sudionike na lokacijama u državi Florida.

Gradovi u državi Florida

Službeni tekst studije (engleski)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of Miami Miller School of Medicine, Miami
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
1 Month – 100 Years · Oba spola · Ažurirano 2. lis 2026. · NCT02450851

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • University of Florida - Neurology, Gainesville
  • USF Ataxia Research Center, Tampa
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
Sve dobne skupine · Oba spola · Ažurirano 1. ruj 2026. · NCT06016946

A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)

  • GC2501 Study Site 103, Gainesville
  • GC2501 Study Site 105, Miami
U tijeku regrutacijaFaza 3
Od 18 do 80 godina · Oba spola · Ažurirano 11. kol 2026. · NCT07555483

Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)

  • The Foundation for Sickle Cell Disease, Hollywood
U tijeku regrutacijaFaza 2
Od 18 godina i više · Oba spola · Ažurirano 5. kol 2026. · NCT07224360

Rett Syndrome Registry

  • Nicklaus Children's Hospital, Miami
U tijeku regrutacijaOpažajna studija
Od 0 do 99 godina · Oba spola · Ažurirano 30. lip 2026. · NCT05432349

A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)

  • Sirven and Associates, Miami
U tijeku regrutacijaOpažajna studija
Od 12 godina i više · Oba spola · Ažurirano 3. lip 2026. · NCT07001280

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

  • Nicklaus Children's Hospital, Miami
  • University of South Florida - 12901 Bruce B Downs, Tampa
U tijeku regrutacijaFaza 1/2
Sve dobne skupine · Oba spola · Ažurirano 22. sij 2026. · NCT04159103

Iz ClinicalTrials.gov, podaci preuzeti 4. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.