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Kliničke studije za Genetski poremećaji u državi Florida
7 studija za Genetski poremećaji traži sudionike na lokacijama u državi Florida.
Gradovi u državi Florida
Službeni tekst studije (engleski)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Miami Miller School of Medicine, Miami
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
1 Month – 100 Years · Oba spola · Ažurirano 2. lis 2026. · NCT02450851Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- University of Florida - Neurology, Gainesville
- USF Ataxia Research Center, Tampa
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
Sve dobne skupine · Oba spola · Ažurirano 1. ruj 2026. · NCT06016946A Non-inferiority Pharmacokinetic and Safety/Tolerability Study of Two Different Doses of Weekly SC Alpha1-PI 15% Compared With Corresponding Standard IV Alpha1-PI in Participants With Alpha1-Antitrypsin Deficiency (AATD)
- GC2501 Study Site 103, Gainesville
- GC2501 Study Site 105, Miami
U tijeku regrutacijaFaza 3
Od 18 do 80 godina · Oba spola · Ažurirano 11. kol 2026. · NCT07555483Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease (SCD)
- The Foundation for Sickle Cell Disease, Hollywood
U tijeku regrutacijaFaza 2
Od 18 godina i više · Oba spola · Ažurirano 5. kol 2026. · NCT07224360Rett Syndrome Registry
- Nicklaus Children's Hospital, Miami
U tijeku regrutacijaOpažajna studija
Od 0 do 99 godina · Oba spola · Ažurirano 30. lip 2026. · NCT05432349A Study Investigating the Effectiveness and Safety of Garadacimab for Treating Patients With Hereditary Angioedema (HAE)
- Sirven and Associates, Miami
U tijeku regrutacijaOpažajna studija
Od 12 godina i više · Oba spola · Ažurirano 3. lip 2026. · NCT07001280Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
- Nicklaus Children's Hospital, Miami
- University of South Florida - 12901 Bruce B Downs, Tampa
U tijeku regrutacijaFaza 1/2
Sve dobne skupine · Oba spola · Ažurirano 22. sij 2026. · NCT04159103Iz ClinicalTrials.gov, podaci preuzeti 4. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.