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Kliničke studije za Rijetke bolesti u državi Kalifornija

10 studija za Rijetke bolesti traži sudionike na lokacijama u državi Kalifornija.

Gradovi u državi Kalifornija

Službeni tekst studije (engleski)

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

  • University of California, Los Angeles, Los Angeles
  • University of California, Irvine Medical Center, Orange
  • Stanford University, Stanford
  • i još 2
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
1 Month – 100 Years · Oba spola · Ažurirano 2. lis 2026. · NCT02450851

A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The University of California, Los Angeles (UCLA), Los Angeles
U tijeku regrutacijaFaza 1
Od 18 do 40 godina · Oba spola · Ažurirano 29. ruj 2026. · NCT07180355

A First-in-human Study of KK8123 in Adults With X-linked Hypophosphatemia

  • University of California - San Francisco, San Francisco
U tijeku regrutacijaFaza 1/2
Od 18 do 65 godina · Oba spola · Ažurirano 21. ruj 2026. · NCT06525636

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • UCLA Ataxia Center, Los Angeles
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
Sve dobne skupine · Oba spola · Ažurirano 1. ruj 2026. · NCT06016946

International Rare Brain Tumor Registry

  • Children's Hospital Los Angeles, Los Angeles
  • University of California San Francisco, San Francisco
U tijeku regrutacijaOpažajna studija
Do 45 godina · Oba spola · Ažurirano 7. kol 2026. · NCT05697874

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of California - Irvine Medical Center, Irvine
U tijeku regrutacijaFaza 2
Od 18 godina i više · Oba spola · Ažurirano 23. lip 2026. · NCT07123155

A Study of AAV9 Gene Therapy in Participants With Canavan Disease (CANaspire Clinical Trial)

  • UCSF Benioff Children's Hospital Oakland, Oakland
U tijeku regrutacijaFaza 1/2
30 Months · Oba spola · Ažurirano 17. tra 2026. · NCT04998396

The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis

  • Children's Hospital of Orange County, Orange
  • UC Irvine, Orange
  • UC Davis, Sacramento
U tijeku regrutacijaFaza 2
Od 12 godina i više · Oba spola · Ažurirano 1. srp 2025. · NCT04372615

Prospective Observational International Registry of Patients With Newly Diagnosed Peripheral T Cell Lymphoma.

  • Stanford University, Stanford
U tijeku regrutacijaOpažajna studija
Od 18 godina i više · Oba spola · Ažurirano 6. svi 2025. · NCT03964480

Epilepsy Learning Healthcare System (ELHS)

  • Children's Hospital Los Angeles, Los Angeles
  • University of Southern California, Los Angeles
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 30. kol 2024. · NCT06265103

Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.