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Kliničke studije za Rijetke bolesti u državi Pennsylvania
7 studija za Rijetke bolesti traži sudionike na lokacijama u državi Pennsylvania.
Gradovi u državi Pennsylvania
Službeni tekst studije (engleski)
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network
- University of Pennsylvania, Philadelphia
- Children's Hospital of Philadelphia, Philadelphia
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
1 Month – 100 Years · Oba spola · Ažurirano 2. lis 2026. · NCT02450851A Study of SGT-212 Gene Therapy in Friedreich's Ataxia
- The Children's Hospital of Philadelphia (CHOP), Philadelphia
U tijeku regrutacijaFaza 1
Od 18 do 40 godina · Oba spola · Ažurirano 29. ruj 2026. · NCT07180355Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study
- Children's Hospital of Philadelphia, Philadelphia
U tijeku regrutacijaOpažajna studijaZdravi dobrovoljci dobrodošli
Sve dobne skupine · Oba spola · Ažurirano 1. ruj 2026. · NCT06016946Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- University of Pennsylvania, Philadelphia
- University of Pittsburgh School of Medicine, Pittsburgh
U tijeku regrutacijaFaza 2
Od 18 godina i više · Oba spola · Ažurirano 23. lip 2026. · NCT07123155A Randomized Study of SPK-10001 Gene Therapy in Participants With Huntington's Disease
- University of Pennsylvania, Philadelphia
- University of Pittsburg, Pittsburgh
U tijeku regrutacijaFaza 1/2
Od 25 do 65 godina · Oba spola · Ažurirano 5. svi 2026. · NCT06826612The ExTINGUISH Trial of Inebilizumab in NMDAR Encephalitis
- University of Pennsylvania, Philadelphia
- University of Pittsburgh, Pittsburgh
U tijeku regrutacijaFaza 2
Od 12 godina i više · Oba spola · Ažurirano 1. srp 2025. · NCT04372615Epilepsy Learning Healthcare System (ELHS)
- Penn State Hershey, Hershey
- Children's Hospital of Philadelphia (CHOP), Philadelphia
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 30. kol 2024. · NCT06265103Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.