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Kliničke studije za Spinalna mišićna atrofija u državi Florida
8 studija za Spinalna mišićna atrofija traži sudionike na lokacijama u državi Florida.
Gradovi u državi Florida
Službeni tekst studije (engleski)
A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
- University of Florida Pediatrics, Gainesville
U tijeku regrutacijaFaza 4
3 Months – 24 Months · Oba spola · Ažurirano 2. lis 2026. · NCT05861986A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophy
- Rare Disease Research FL LLC, Kissimmee
U tijeku regrutacijaFaza 2
Od 5 do 17 godina · Oba spola · Ažurirano 14. ruj 2026. · NCT07287982A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
- University of Florida Pediatrics, Gainesville
U tijeku regrutacijaFaza 4
3 Months – 24 Months · Oba spola · Ažurirano 10. ruj 2026. · NCT05861999A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
- Nemours Children's Hospital, Orlando, Orlando
U tijeku regrutacijaFaza 1
Od 3 godina i više · Oba spola · Ažurirano 3. ruj 2026. · NCT06555419Study of an Intrathecal Port and Catheter System for Subjects With Spinal Muscular Atrophy
- Nemours Children's Hospital, Florida, Orlando
U tijeku regrutacija
Od 3 godina i više · Oba spola · Ažurirano 19. kol 2026. · NCT05866419Clinical Procedures to Support Research in ALS
- University of Miami, Miami
U tijeku regrutacijaOpažajna studija
Od 18 godina i više · Oba spola · Ažurirano 15. lip 2026. · NCT03489278ALS/MND Natural History Study Data Repository
- University of Florida, Gainesville
U tijeku regrutacijaOpažajna studija
Od 18 do 90 godina · Oba spola · Ažurirano 20. svi 2026. · NCT05966038Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA)
- Golisano Children's Hospital of Southwest Florida, Fort Myers
- Jackson South Medical Center, Palmetto Bay
U tijeku regrutacijaOpažajna studija
Sve dobne skupine · Oba spola · Ažurirano 31. sij 2025. · NCT04174157Iz ClinicalTrials.gov, podaci preuzeti 5. lis 2026.. Svaka studija ima svoje uvjete prihoda; tim studije odlučuje tko se može priključiti.