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Etid klinik pou Ataksi nan Pennsylvania

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A Study of SGT-212 Gene Therapy in Friedreich's Ataxia

  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Ap rekriteFaz 1
Laj 18 a 40 · Tout sèks · Mizajou Sep 29, 2026 · NCT07180355

Prospective Natural History Study of POLG Disease

  • Children's Hospital of Philadelphia-Philadelphia, Philadelphia
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Sep 15, 2026 · NCT07775872

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

  • Children's Hospital of Philadelphia, Philadelphia
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Tout laj · Tout sèks · Mizajou Sep 1, 2026 · NCT06016946

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.