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Etid klinik pou Distrofi Miskilè Duchenne nan Kalifòni

6 etid pou Distrofi Miskilè Duchenne ap chèche patisipan nan sit nan Kalifòni.

Vil nan Kalifòni

Tèks ofisyèl etid la (Anglè)

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

  • Loma Linda University Pediatric Subspecialty Clinics, Loma Linda
  • Children's Hospital Los Angeles, Los Angeles
  • Valley Children's Hospital, Madera
  • ak 2 plis
Ap rekriteEtid obsèvasyon
Laj 2 ak plis · Gason · Mizajou Sep 24, 2026 · NCT06564974

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

  • University of California, San Diego, La Jolla
  • University of California, Los Angeles, Los Angeles
  • Stanford University, Palo Alto
  • ak 1 plis
Ap rekriteFaz 1
Laj 2 ak plis · Gason · Mizajou Sep 11, 2026 · NCT04626674

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

  • UC Davis, Sacramento
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jul 28, 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

  • University of California, Los Angeles Medical Center, Los Angeles
  • University of California, Davis, Sacramento
  • University of California, San Diego
Ap rekriteFaz 1/2
Laj 0 a 17 · Gason · Mizajou Jul 8, 2026 · NCT06138639

Duchenne Electronic Health Record Study

  • UC Davis Health, Sacramento
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou May 27, 2026 · NCT07609394

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

  • Stanford University, Palo Alto
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 5 ak plis · Tout sèks · Mizajou Apr 9, 2026 · NCT06839469

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.