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Etid klinik pou Distrofi Miskilè Duchenne ap rekrite nan Etazini

26 etid pou Distrofi Miskilè Duchenne ap rekrite patisipan nan sit atravè Etazini.

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Tèks ofisyèl etid la (Anglè)

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

Ap rekriteFaz 3
Laj 7 a 11 · Gason · Mizajou Sep 28, 2026 · NCT07160634

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

Ap rekriteEtid obsèvasyon
Laj 2 ak plis · Gason · Mizajou Sep 24, 2026 · NCT06564974

Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy

Ap rekriteFaz 1
Laj 8 a 18 · Gason · Mizajou Aug 24, 2026 · NCT07172971

Once Weekly Infant Corticosteroid Trial for DMD

Ap rekriteFaz 4
1 Month – 30 Months · Gason · Mizajou Aug 14, 2026 · NCT05412394

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jul 28, 2026 · NCT07674758

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

Ap rekriteFaz 1/2
Laj 0 a 17 · Gason · Mizajou Jul 8, 2026 · NCT06138639

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

Ap rekriteEtid obsèvasyon
Laj 6 ak plis · Tout sèks · Mizajou Jul 2, 2026 · NCT07127978

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

Ap rekriteFaz 1/2
Laj 2 a 7 · Gason · Mizajou Jun 23, 2026 · NCT07429240

Duchenne Electronic Health Record Study

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou May 27, 2026 · NCT07609394

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 10 ak plis · Gason · Mizajou May 22, 2026 · NCT06124196

Vasodilator and Exercise Study for DMD (VASO-REx)

Ap rekriteFaz 2
Laj 6 ak plis · Gason · Mizajou May 15, 2026 · NCT06290713

The Duchenne Registry

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou May 8, 2026 · NCT02069756

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 5 ak plis · Tout sèks · Mizajou Apr 9, 2026 · NCT06839469

Urinary Titin Biomarker in DMD

Ap rekriteVolontè an sante akeyi
Laj 2 a 10 · Gason · Mizajou Apr 8, 2026 · NCT07332013

Trial of Cell Based Therapy for DMD

Ap rekriteFaz 1
Laj 18 ak plis · Tout sèks · Mizajou Mar 4, 2026 · NCT06692426

Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

Ap rekriteFaz 1/2
Laj 4 a 18 · Gason · Mizajou Dec 15, 2025 · NCT04906460

Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy

Ap rekriteEtid obsèvasyon
Laj 5 ak plis · Tout sèks · Mizajou Nov 24, 2025 · NCT05016908

Biomarker Development for Muscular Dystrophies

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 5 ak plis · Tout sèks · Mizajou Nov 24, 2025 · NCT05019625

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim

Ap rekriteEtid obsèvasyon
Laj 10 ak plis · Gason · Mizajou Nov 6, 2025 · NCT06093100

Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 5 a 62 · Gason · Mizajou Oct 15, 2025 · NCT01484678

DMD Voice: Qualitative Interviews With Patients and Caregivers

Ap rekriteEtid obsèvasyon
Laj 10 ak plis · Gason · Mizajou Apr 30, 2025 · NCT06925269

Sous ClinicalTrials.gov, done yo ranmase Oct 3, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.