Akèy › Distrofi Miskilè Duchenne › Missouri
Etid klinik pou Distrofi Miskilè Duchenne nan Missouri
3 etid pou Distrofi Miskilè Duchenne ap chèche patisipan nan sit nan Missouri.
Vil nan Missouri
Tèks ofisyèl etid la (Anglè)
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
- Washington University in St. Louis, St Louis
Ap rekriteFaz 1
Laj 2 ak plis · Gason · Mizajou Sep 11, 2026 · NCT04626674A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)
- Washington University in St. Louis, St Louis
Ap rekriteFaz 1/2
Laj 0 a 17 · Gason · Mizajou Jul 8, 2026 · NCT06138639PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)
- Washington University School of Medicine, St Louis
Ap rekriteFaz 1/2
Laj 2 a 7 · Gason · Mizajou Jun 23, 2026 · NCT07429240Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.