Akèy › Distrofi Miskilè Duchenne › North Carolina
Etid klinik pou Distrofi Miskilè Duchenne nan North Carolina
6 etid pou Distrofi Miskilè Duchenne ap chèche patisipan nan sit nan North Carolina.
Vil nan North Carolina
Tèks ofisyèl etid la (Anglè)
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
- Duke University Medical Center, Durham
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Laj 2 ak plis · Gason · Mizajou Sep 11, 2026 · NCT04626674Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials
- Duke Children's Hospital, Durham
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jul 28, 2026 · NCT07674758A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy
- Duke University / Lenox Baker Children's Hospital, Durham
Ap rekriteEtid obsèvasyon
Laj 6 ak plis · Tout sèks · Mizajou Jul 2, 2026 · NCT07127978Duchenne Electronic Health Record Study
- Duke University Medical Center, Durham
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou May 27, 2026 · NCT07609394Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)
- Rare Disease Research, LLC, Hillsborough
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Laj 4 a 18 · Gason · Mizajou May 27, 2026 · NCT07608432Biomarker Development for Muscular Dystrophies
- Wake Forest University, Winston-Salem
Ap rekriteEtid obsèvasyonVolontè an sante akeyi
Laj 5 ak plis · Tout sèks · Mizajou Nov 24, 2025 · NCT05019625Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.