Akèy › Maladi Gaucher
Etid klinik pou Maladi Gaucher ap rekrite nan Etazini
14 etid pou Maladi Gaucher ap rekrite patisipan nan sit atravè Etazini.
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Tèks ofisyèl etid la (Anglè)
Gaucher Disease Outcome Survey (GOS)
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Tout laj · Tout sèks · Mizajou Sep 15, 2026 · NCT03291223A Long-term Follow-up Study of Gaucher Disease
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Tout laj · Tout sèks · Mizajou Sep 3, 2026 · NCT03190837A Gaucher Disease Gene Therapy Trial With FLT201
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Laj 18 ak plis · Tout sèks · Mizajou Sep 3, 2026 · NCT07223944Advancing Integrated Therapies for Gaucher Disease
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3 Months – 75 Years · Tout sèks · Mizajou Aug 11, 2026 · NCT07758816MAGNETIC RESONANCE SPECTROSCOPY BIOMARKERS IN TYPE 3 GAUCHER DISEASE (GD3)
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Laj 18 a 80 · Tout sèks · Mizajou Aug 4, 2026 · NCT05586243Oxidative Stress and Inflammatory Biomarkers in Gaucher Disease
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Laj 18 a 75 · Tout sèks · Mizajou Jul 13, 2026 · NCT02437396International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
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Tout laj · Tout sèks · Mizajou Apr 14, 2026 · NCT00358943Registry of Patients Diagnosed With Lysosomal Storage Diseases
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Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900Extracellular Vesicles as Potential Biomarkers and Therapeutic Target in Gaucher Disease
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Laj 18 a 80 · Tout sèks · Mizajou Apr 6, 2026 · NCT05843552Study of CAR T-Cells Targeting the GD2 With IL-15+iCaspase9 for Relapsed/Refractory Neuroblastoma or Relapsed/Refractory Osteosarcoma
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18 Months · Tout sèks · Mizajou Mar 27, 2026 · NCT03721068PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
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Laj 18 a 50 · Fanm · Mizajou Mar 17, 2026 · NCT04532047Longitudinal Study of Neurodegenerative Disorders
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Tout laj · Tout sèks · Mizajou Feb 9, 2026 · NCT03333200Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC
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2 Months – 60 Years · Tout sèks · Mizajou Jan 13, 2026 · NCT04528355Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT
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2 Months – 55 Years · Tout sèks · Mizajou Dec 15, 2025 · NCT01962415Sous ClinicalTrials.gov, done yo ranmase Oct 1, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.