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Etid klinik pou Maladi Gaucher nan Kalifòni

4 etid pou Maladi Gaucher ap chèche patisipan nan sit nan Kalifòni.

Vil nan Kalifòni

Tèks ofisyèl etid la (Anglè)

A Gaucher Disease Gene Therapy Trial With FLT201

  • Kaiser Permanente - CA, Los Angeles
  • UCLA Health, Los Angeles
  • University of California, San Francisco (UCSF), San Francisco
Ap rekriteFaz 3
Laj 18 ak plis · Tout sèks · Mizajou Sep 3, 2026 · NCT07223944

International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry

  • Tower Hematology Oncology Medical Group- Site Number : 840056, Beverly Hills
  • University of California at Irvine- Site Number : 840036, Irvine
  • Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
  • ak 4 plis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Apr 14, 2026 · NCT00358943

Registry of Patients Diagnosed With Lysosomal Storage Diseases

  • University of California San Francisco, San Francisco
Ap rekriteEtid obsèvasyon
Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900

PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)

  • University of California, San Francisco
Ap rekriteFaz 1
Laj 18 a 50 · Fanm · Mizajou Mar 17, 2026 · NCT04532047

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.