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Etid klinik pou Maladi Gaucher nan Kalifòni
4 etid pou Maladi Gaucher ap chèche patisipan nan sit nan Kalifòni.
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A Gaucher Disease Gene Therapy Trial With FLT201
- Kaiser Permanente - CA, Los Angeles
- UCLA Health, Los Angeles
- University of California, San Francisco (UCSF), San Francisco
Ap rekriteFaz 3
Laj 18 ak plis · Tout sèks · Mizajou Sep 3, 2026 · NCT07223944International Collaborative Gaucher Group (ICGG) Gaucher Disease Registry & Pregnancy Sub-registry
- Tower Hematology Oncology Medical Group- Site Number : 840056, Beverly Hills
- University of California at Irvine- Site Number : 840036, Irvine
- Southern California Permanente Medical Group- Site Number : 840108, Los Angeles
- ak 4 plis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Apr 14, 2026 · NCT00358943Registry of Patients Diagnosed With Lysosomal Storage Diseases
- University of California San Francisco, San Francisco
Ap rekriteEtid obsèvasyon
Jiska laj 64 · Tout sèks · Mizajou Apr 8, 2026 · NCT05619900PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
- University of California, San Francisco
Ap rekriteFaz 1
Laj 18 a 50 · Fanm · Mizajou Mar 17, 2026 · NCT04532047Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.