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Akèy › Twoub Jenetik › Pennsylvania › Philadelphia

Etid klinik pou Twoub Jenetik nan Philadelphia, PA

9 etid pou Twoub Jenetik ap chèche patisipan nan sit nan ak bò kote Philadelphia (nan yon distans apeprè 30 mil). Louvri yon etid pou wè ki moun ki ka patisipe ak kijan pou kontakte ekip etid la.

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Ap chèche patisipan pou yon etid? Mete l anwo paj sa a — $99 pou 30 jou →

Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases Network

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
  • University of Pennsylvania, Philadelphia
  • Children's Hospital of Philadelphia, Philadelphia
1 Month – 100 Years · Tout sèks · Mizajou Oct 2, 2026 · NCT02450851

Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia

Ap rekriteFaz 2/3
  • Children's Hospital of Philadelphia, Philadelphia
  • Nemours Children's Health, Wilmington · 25 mi lwen
Laj 2 a 17 · Tout sèks · Mizajou Sep 24, 2026 · NCT07441876

Friedreich Ataxia Global Clinical Consortium UNIFIED Natural History Study

Ap rekriteEtid obsèvasyonVolontè an sante akeyi
  • Children's Hospital of Philadelphia, Philadelphia
Tout laj · Tout sèks · Mizajou Sep 1, 2026 · NCT06016946

Rett Syndrome Registry

Ap rekriteEtid obsèvasyon
  • Children's Hospital of Philadelphia, Philadelphia
Laj 0 a 99 · Tout sèks · Mizajou Jun 30, 2026 · NCT05432349

Rifampin in CYP24A1-related Hypercalcemia and Hypercalciuria

Ap rekriteFaz 2
  • Children's Hospital of Philadelphia, Philadelphia
6 Months – 65 Years · Tout sèks · Mizajou Jun 22, 2026 · NCT03301038

ARPKD Database Study

Ap rekriteEtid obsèvasyon
  • Children's Hospital of Philadelphia, Philadelphia
Jiska laj 18 · Tout sèks · Mizajou Jun 15, 2026 · NCT01401998

A Study to Assess the Long-term Safety and Clinical Activity of mRNA-3927 in Participants Previously Enrolled in the mRNA-3927-P101 Study

Ap rekriteFaz 1/2
  • The Children's Hospital of Philadelphia (CHOP), Philadelphia
Laj 1 ak plis · Tout sèks · Mizajou Mar 23, 2026 · NCT05130437

Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia

Ap rekriteFaz 1/2
  • Children's Hospital of Philadelphia (CHOP), Philadelphia
Tout laj · Tout sèks · Mizajou Jan 22, 2026 · NCT04159103

STXBP1 and SYNGAP1 Related Disorders Natural History Study

Ap rekriteEtid obsèvasyon
  • The Children's Hospital of Philadelphia, Philadelphia
Tout laj · Tout sèks · Mizajou Oct 29, 2025 · NCT06555965

Etid Twoub Jenetik nan lòt vil

Lòt etid nan Philadelphia

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.