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Etid klinik pou Maladi Depo Glikojèn Tip II nan Arizona
3 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan Arizona.
Vil nan Arizona
Tèks ofisyèl etid la (Anglè)
A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
- Barrow Neurological Institute, Phoenix
Ap rekriteFaz 1/2
Laj 18 a 65 · Tout sèks · Mizajou Jul 20, 2026 · NCT07282847Pompe Disease Registry Protocol
- Barrow Neurological Institute- Site Number : 840087, Phoenix
- Phoenix Children's Hospital- Site Number : 840003, Phoenix
- University of Arizona- Site Number : 840015, Tucson
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400Pompe Pregnancy Sub-Registry
- Barrow Neurol Group- Site Number : 840087, Phoenix
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Apr 16, 2026 · NCT00567073Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.