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Etid klinik pou Maladi Depo Glikojèn Tip II ap rekrite nan Etazini

10 etid pou Maladi Depo Glikojèn Tip II ap rekrite patisipan nan sit atravè Etazini.

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Pompe Disease Registry Protocol

Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155

Pompe Pregnancy Sub-Registry

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Tout laj · Fanm · Mizajou Apr 16, 2026 · NCT00567073

Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease

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Tout laj · Tout sèks · Mizajou Apr 8, 2026 · NCT01665326

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

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Laj 18 ak plis · Tout sèks · Mizajou Mar 17, 2026 · NCT07478172

A Global Prospective Observational Registry of Patients With Pompe Disease

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Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011

Cognitive and Neurological Pathologies in Pompe Disease

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Laj 0 a 18 · Tout sèks · Mizajou Mar 4, 2026 · NCT04639336

Avalglucosidase Alfa Pregnancy Study

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Tout laj · Fanm · Mizajou Jan 16, 2026 · NCT05734521

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.