Akèy › Maladi Depo Glikojèn Tip II
Etid klinik pou Maladi Depo Glikojèn Tip II ap rekrite nan Etazini
10 etid pou Maladi Depo Glikojèn Tip II ap rekrite patisipan nan sit atravè Etazini.
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- Durham, NC8 etid
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Etid ki fèk mete ajou
Tèks ofisyèl etid la (Anglè)
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
Ap rekriteFaz 1
Laj 18 a 75 · Tout sèks · Mizajou Aug 17, 2026 · NCT07354724A Study to Evaluate Safety, Tolerability, and Efficacy of AB-1009 Gene Therapy (GAA Gene) in Adult Participants With Late-Onset Pompe Disease (PROGRESS-GT LOPD)
Ap rekriteFaz 1/2
Laj 18 a 65 · Tout sèks · Mizajou Jul 20, 2026 · NCT07282847Pompe Disease Registry Protocol
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155Pompe Pregnancy Sub-Registry
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Apr 16, 2026 · NCT00567073Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Apr 8, 2026 · NCT01665326Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
Ap rekrite
Laj 18 ak plis · Tout sèks · Mizajou Mar 17, 2026 · NCT07478172A Global Prospective Observational Registry of Patients With Pompe Disease
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011Cognitive and Neurological Pathologies in Pompe Disease
Ap rekriteEtid obsèvasyon
Laj 0 a 18 · Tout sèks · Mizajou Mar 4, 2026 · NCT04639336Avalglucosidase Alfa Pregnancy Study
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Jan 16, 2026 · NCT05734521Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.