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Etid klinik pou Maladi Depo Glikojèn Tip II nan Florid

4 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan Florid.

Vil nan Florid

Tèks ofisyèl etid la (Anglè)

Pompe Disease Registry Protocol

  • University of Miami- Site Number : 840006, Coral Gables
  • University of Florida College of Medicine- Site Number : 840012, Gainesville
  • University of Florida Pediatrics Genetics- Site Number : 840121, Jacksonville
  • ak 1 plis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • University of Florida (UF) - Gainesville, Gainesville
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155

Pompe Pregnancy Sub-Registry

  • University of Florida Pediatrics Genetics- Site Number : 157138, Jacksonville
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Apr 16, 2026 · NCT00567073

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Wolfson Children's Hospital, Jacksonville
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.