Akèy › Maladi Depo Glikojèn Tip II › Missouri
Etid klinik pou Maladi Depo Glikojèn Tip II nan Missouri
6 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan Missouri.
Vil nan Missouri
Tèks ofisyèl etid la (Anglè)
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
- Washington University School of Medicine, St Louis
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Laj 18 a 75 · Tout sèks · Mizajou Aug 17, 2026 · NCT07354724Pompe Disease Registry Protocol
- University of Missouri Health System Department of Genetics- Site Number : 840031, Columbia
- Washington University- Site Number : 840100, St Louis
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Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
- Washington University in St. Louis, St Louis
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155Pompe Pregnancy Sub-Registry
- Washington University- Site Number : 150612, St Louis
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Tout laj · Fanm · Mizajou Apr 16, 2026 · NCT00567073Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease
- NextGen Precision Health Building, Clinical and Translational Science Unit, Columbia
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Laj 18 ak plis · Tout sèks · Mizajou Mar 17, 2026 · NCT07478172A Global Prospective Observational Registry of Patients With Pompe Disease
- Washington University School of Medicine, St Louis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.