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Etid klinik pou Maladi Depo Glikojèn Tip II nan Missouri

6 etid pou Maladi Depo Glikojèn Tip II ap chèche patisipan nan sit nan Missouri.

Vil nan Missouri

Tèks ofisyèl etid la (Anglè)

A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease

  • Washington University School of Medicine, St Louis
Ap rekriteFaz 1
Laj 18 a 75 · Tout sèks · Mizajou Aug 17, 2026 · NCT07354724

Pompe Disease Registry Protocol

  • University of Missouri Health System Department of Genetics- Site Number : 840031, Columbia
  • Washington University- Site Number : 840100, St Louis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Jun 23, 2026 · NCT00231400

Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)

  • Washington University in St. Louis, St Louis
Ap rekriteFaz 2
Laj 18 ak plis · Tout sèks · Mizajou Jun 23, 2026 · NCT07123155

Pompe Pregnancy Sub-Registry

  • Washington University- Site Number : 150612, St Louis
Ap rekriteEtid obsèvasyon
Tout laj · Fanm · Mizajou Apr 16, 2026 · NCT00567073

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

  • NextGen Precision Health Building, Clinical and Translational Science Unit, Columbia
Ap rekrite
Laj 18 ak plis · Tout sèks · Mizajou Mar 17, 2026 · NCT07478172

A Global Prospective Observational Registry of Patients With Pompe Disease

  • Washington University School of Medicine, St Louis
Ap rekriteEtid obsèvasyon
Tout laj · Tout sèks · Mizajou Mar 10, 2026 · NCT06121011

Sous ClinicalTrials.gov, done yo ranmase Oct 5, 2026. Chak etid gen kritè li pou li menm; ekip etid la deside ki moun ki ka patisipe.